Department of Pediatric Hematology and Oncology
Publications
- 2020
Rare non-Hodgkin lymphoma of childhood and adolescence: A consensus diagnostic and therapeutic approach to pediatric-type follicular lymphoma, marginal zone lymphoma, and nonanaplastic peripheral T-cell lymphoma
Attarbaschi, A., Abla, O., Arias Padilla, L., Beishuizen, A., Burke, G. A. A., Brugières, L., Bruneau, J., Burkhardt, B., d'Amore, E. S. G., Klapper, W., Kontny, U., Pillon, M., Taj, M., Turner, S. D., Uyttebroeck, A., Woessmann, W. & Mellgren, K., 08.2020, In: PEDIATR BLOOD CANCER. 67, 8, p. e28416Research output: SCORING: Contribution to journal › SCORING: Review article › Research
DNA binds to a specific site of the adhesive blood-protein von Willebrand factor guided by electrostatic interactions
Sandoval-Pérez, A., Berger, R. M. L., Garaizar, A., Farr, S. E., Brehm, M. A., König, G., Schneider, S. W., Collepardo-Guevara, R., Huck, V., Rädler, J. O. & Aponte-Santamaría, C., 27.07.2020, In: NUCLEIC ACIDS RES. 48, 13, p. 7333-7344 12 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Accurate In-Vivo Quantification of CD19 CAR-T Cells after Treatment with Axicabtagene Ciloleucel (Axi-Cel) and Tisagenlecleucel (Tisa-Cel) Using Digital PCR
Badbaran, A., Berger, C., Riecken, K., Kruchen, A., Geffken, M., Müller, I., Kröger, N., Ayuk, F. A. & Fehse, B., 20.07.2020, In: CANCERS. 12, 7Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Age and DNA-methylation subgroup as potential independent risk factors for treatment stratification in children with Atypical Teratoid/Rhabdoid Tumors (ATRT)
Frühwald, M. C., Hasselblatt, M., Nemes, K., Bens, S., Steinbügl, M., Johann, P. D., Kerl, K., Hauser, P., Quiroga, E., Solano-Paez, P., Biassoni, V., Gil-da-Costa, M. J., Perek-Polnik, M., van de Wetering, M., Sumerauer, D., Pears, J., Stabell, N., Holm, S., Hengartner, H., Gerber, N. U., Grotzer, M., Boos, J., Ebinger, M., Tippelt, S., Paulus, W., Furtwängler, R., Hernáiz-Driever, P., Reinhard, H., Rutkowski, S., Schlegel, P-G., Schmid, I., Kortmann, R-D., Timmermann, B., Warmuth-Metz, M., Kordes, U., Gerss, J., Nysom, K., Schneppenheim, R., Siebert, R., Kool, M. & Graf, N., 07.07.2020, In: NEURO-ONCOLOGY. 22, 7, p. 1006–1017 12 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Genome-wide DNA methylation profiles distinguish silent from non-silent ACTH adenomas
Ricklefs, F. L., Fita, K. D., Rotermund, R., Piffko, A., Schmid, S., Capper, D., Buslei, R., Buchfelder, M., Burkhardt, T., Matschke, J., Lamszus, K., Westphal, M., Schüller, U. & Flitsch, J., 07.2020, In: ACTA NEUROPATHOL. 140, 1, p. 95-97 3 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Incidence of SCID in Germany from 2014 to 2015 an ESPED* Survey on Behalf of the API*** Erhebungseinheit für Seltene Pädiatrische Erkrankungen in Deutschland (German Paediatric Surveillance Unit) ** Arbeitsgemeinschaft Pädiatrische Immunologie
Shai, S., Perez-Becker, R., Andres, O., Bakhtiar, S., Bauman, U., von Bernuth, H., Classen, C-F., Dückers, G., El-Helou, S. M., Gangfuß, A., Ghosh, S., Grimbacher, B., Hauck, F., Hoenig, M., Husain, R. A., Kindle, G., Kipfmueller, F., Klemann, C., Krüger, R., Lainka, E., Lehmberg, K., Lohrmann, F., Morbach, H., Naumann-Bartsch, N., Oommen, P. T., Schulz, A., Seidemann, K., Speckmann, C., Sykora, K-W., von Kries, R. & Niehues, T., 07.2020, In: J CLIN IMMUNOL. 40, 5, p. 708-717 10 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Infant high grade gliomas comprise multiple subgroups characterized by novel targetable gene fusions and favorable outcomes
Clarke, M., Mackay, A., Ismer, B., Pickles, J. C., Tatevossian, R. G., Newman, S., Bale, T. A., Stoler, I., Izquierdo, E., Temelso, S., Carvalho, D. M., Molinari, V., Burford, A., Howell, L., Virasami, A., Fairchild, A. R., Avery, A., Chalker, J., Kristiansen, M., Haupfear, K., Dalton, J. D., Orisme, W., Wen, J., Hubank, M., Kurian, K. M., Rowe, C., Maybury, M., Crosier, S., Knipstein, J., Schuller, U., Kordes, U., Kram, D. E., Snuderl, M., Bridges, L., Martin, A. J., Doey, L. J., Al-Sarraj, S., Chandler, C., Zebian, B., Cairns, C., Natrajan, R., Boult, J. K., Robinson, S. P., Sill, M., Dunkel, I. J., Gilheeney, S. W., Rosenblum, M. K., Hughes, D., Proszek, P. Z., MacDonald, T. J., Preusser, M., Haberler, C., Slavc, I., Packer, R., Ng, H-K., Caspi, S., Popovic, M., Faganel Kotnik, B., Wood, M. D., Baird, L., Davare, M. A., Solomon, D. A., Olsen, T. K., Brandal, P., Farrell, M., Cryan, J. B., Capra, M., Karremann, M., Schittenhelm, J., Schuhmann, M. U., Ebinger, M., Dinjens, W. N. M., Kerl, K., Hettmer, S., Pietsch, T., Andreiuolo, F., Driever, P. H., Korshunov, A., Hiddingh, L., Worst, B. C., Sturm, D., Zuckermann, M., Witt, O., Bloom, T., Mitchell, C., Miele, E., Colafati, G. S., Diomedi-Camassei, F., Bailey, S., Moore, A. S., Hassall, T. E., Lowis, S. P., Tsoli, M., Cowley, M. J., Ziegler, D. S., Karajannis, M. A., Aquilina, K., Hargrave, D. R., Carceller, F., Marshall, L. V., von Deimling, A., Kramm, C. M., Pfister, S. M., Sahm, F., Baker, S. J., Mastronuzzi, A., Carai, A., Vinci, M., Capper, D., Popov, S., Ellison, D. W., Jacques, T. S., Jones, D. T. W. & Jones, C., 07.2020, In: CANCER DISCOV. 10, 7, p. 942-963 22 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Nonmetastatic Medulloblastoma of Early Childhood: Results From the Prospective Clinical Trial HIT-2000 and An Extended Validation Cohort
Mynarek, M., von Hoff, K., Pietsch, T., Ottensmeier, H., Warmuth-Metz, M., Bison, B., Pfister, S., Korshunov, A., Sharma, T., Jaeger, N., Ryzhova, M., Zheludkova, O., Golanov, A., Rushing, E. J., Hasselblatt, M., Koch, A., Schüller, U., von Deimling, A., Sahm, F., Sill, M., Riemenschneider, M. J., Dohmen, H., Monoranu, C. M., Sommer, C., Staszewski, O., Mawrin, C., Schittenhelm, J., Brück, W., Filipski, K., Hartmann, C., Meinhardt, M., Pietschmann, K., Haberler, C., Slavc, I., Gerber, N. U., Grotzer, M., Benesch, M., Schlegel, P. G., Deinlein, F., von Bueren, A. O., Friedrich, C., Juhnke, B-O., Obrecht, D., Fleischhack, G., Kwiecien, R., Faldum, A., Kortmann, R. D., Kool, M. & Rutkowski, S., 20.06.2020, In: J CLIN ONCOL. 38, 18, p. 2028-2040 13 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Flash survey on severe acute respiratory syndrome coronavirus-2 infections in paediatric patients on anticancer treatment
Hrusak, O., Kalina, T., Wolf, J., Balduzzi, A., Provenzi, M., Rizzari, C., Rives, S., Del Pozo Carlavilla, M., Alonso, M. E. V., Domínguez-Pinilla, N., Bourquin, J-P., Schmiegelow, K., Attarbaschi, A., Grillner, P., Mellgren, K., van der Werff Ten Bosch, J., Pieters, R., Brozou, T., Borkhardt, A., Escherich, G., Lauten, M., Stanulla, M., Smith, O., Yeoh, A. E. J., Elitzur, S., Vora, A., Li, C-K., Ariffin, H., Kolenova, A., Dallapozza, L., Farah, R., Lazic, J., Manabe, A., Styczynski, J., Kovacs, G., Ottoffy, G., Felice, M. S., Buldini, B., Conter, V., Stary, J. & Schrappe, M., 06.2020, In: EUR J CANCER. 132, p. 11-16 6 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Hemophagocytic Lymphohistiocytosis in Critically Ill Patients
Knaak, C., Schuster, F. S., Spies, C., Vorderwülbecke, G., Nyvlt, P., Schenk, T., Balzer, F., La Rosée, P., Janka, G., Brunkhorst, F. M., Keh, D. & Lachmann, G., 06.2020, In: SHOCK. 53, 6, p. 701-709 9 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Influence of anti-thymocyte globulin plasma levels on outcome parameters in stem cell transplanted children
Vogelsang, V., Kruchen, A., Wustrau, K., Spohn, M. & Müller, I., 06.2020, In: INT IMMUNOPHARMACOL. 83, p. 106371Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
The basic helix-loop-helix transcription factor TCF4 impacts brain architecture as well as neuronal morphology and differentiation
Schoof, M., Hellwig, M., Harrison, L., Holdhof, D., Lauffer, M. C., Niesen, J., Virdi, S., Indenbirken, D. & Schüller, U., 06.2020, In: EUR J NEUROSCI. 51, 11, p. 2219-2235 17 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Can we optimise doxorubicin treatment regimens for children with cancer? Pharmacokinetic simulations and a Delphi consensus procedure
Siebel, C., Würthwein, G., Lanvers-Kaminsky, C., André, N., Berthold, F., Castelli, I., Chastagner, P., Doz, F., English, M., Escherich, G., Frühwald, M. C., Graf, N., Groll, A. H., Ruggiero, A., Hempel, G. & Boos, J., 28.05.2020, In: BMC PHARMACOL TOXICO. 21, 1, p. 37Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Hemophagocytic lymphohistiocytosis in critically ill patients: diagnostic reliability of HLH-2004 criteria and HScore
Knaak, C., Nyvlt, P., Schuster, F. S., Spies, C., Heeren, P., Schenk, T., Balzer, F., La Rosée, P., Janka, G., Brunkhorst, F. M., Keh, D. & Lachmann, G., 24.05.2020, In: CRIT CARE. 24, 1, p. 244Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Targeted busulfan-based reduced-intensity conditioning and HLA-matched HSCT cure hemophagocytic lymphohistiocytosis
Felber, M., Steward, C. G., Kentouche, K., Fasth, A., Wynn, R. F., Zeilhofer, U., Haunerdinger, V., Volkmer, B., Prader, S., Gruhn, B., Ehl, S., Lehmberg, K., Müller, D., Gennery, A. R., Albert, M. H., Hauck, F., Rao, K., Veys, P., Hassan, M., Lankester, A. C., Schmid, J. P., Hauri-Hohl, M. M. & Güngör, T., 12.05.2020, In: BLOOD ADV. 4, 9, p. 1998-2010 13 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Pik3ca mutations significantly enhance the growth of Shh medulloblastoma and lead to metastatic tumour growth in a novel mouse model
Niesen, J., Ohli, J., Sedlacik, J., Dührsen, L., Hellwig, M., Spohn, M., Holsten, T. & Schüller, U., 01.05.2020, In: CANCER LETT. 477, p. 10-18 9 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
An 8-Year-Old Girl with Posterior Fossa Mass
Ruf, V. C., Schöler, A., Capper, D., Arzberger, T., Herms, J. & Schüller, U., 05.2020, In: BRAIN PATHOL. 30, 3, p. 713-714 2 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Epigenetics impacts upon prognosis and clinical management of choroid plexus tumors
Thomas, C., Metrock, K., Kordes, U., Hasselblatt, M. & Dhall, G., 05.2020, In: J NEURO-ONCOL. 148, 1, p. 39-45 7 p.Research output: SCORING: Contribution to journal › SCORING: Review article › Research
Macrophage-tumor cell interaction promotes ATRT progression and chemoresistance
Melcher, V., Graf, M., Interlandi, M., Moreno, N., de Faria, F. W., Kim, S. N., Kastrati, D., Korbanka, S., Alfert, A., Gerß, J., Meyer Zu Hörste, G., Hartmann, W., Frühwald, M. C., Dugas, M., Schüller, U., Hasselblatt, M., Albert, T. K. & Kerl, K., 05.2020, In: ACTA NEUROPATHOL. 139, 5, p. 913-936 24 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Preferential sensitivity to HDAC inhibitors in tumors with CREBBP mutation
Hellwig, M., Merk, D. J., Lutz, B. & Schüller, U., 05.2020, In: CANCER GENE THER. 27, 5, p. 294-300 7 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Register und Studien in der Gesellschaft für Pädiatrische Onkologie und Hämatologie (GPOH) – Welchen Beitrag leisten sie zum Fortschritt?
Klingebiel, T., Jürgens, H., Glauche, I., Gnekow, A., Kandels, D., Woessmann, W., Schneider, D. T. & Suttorp, M., 05.2020, In: KLIN PADIATR. 232, 3, p. 124-135 12 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Favorable outcomes of hematopoietic stem cell transplantation in children and adolescents with Diamond-Blackfan anemia
Strahm, B., Loewecke, F., Niemeyer, C. M., Albert, M., Ansari, M., Bader, P., Bertrand, Y., Burkhardt, B., Da Costa, L. M., Ferster, A., Fischer, A., Güngör, T., Gruhn, B., Hainmann, I., Kapp, F., Lang, P., Müller, I., Schulz, A., Szvetnik, A., Wlodarski, M., Noellke, P., Leblanc, T. & Dalle, J-H., 28.04.2020, In: BLOOD ADV. 4, 8, p. 1760-1769 10 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
A validated novel continuous prognostic index to deliver stratified medicine in pediatric acute lymphoblastic leukemia
Enshaei, A., O'Connor, D., Bartram, J., Hancock, J., Harrison, C. J., Hough, R., Samarasinghe, S., den Boer, M. L., Boer, J. M., de Groot-Kruseman, H. A., Marquart, H. V., Noren-Nystrom, U., Schmiegelow, K., Schwab, C., Horstmann, M. A., Escherich, G., Heyman, M., Pieters, R., Vora, A., Moppett, J. & Moorman, A. V., 23.04.2020, In: BLOOD. 135, 17, p. 1438-1446 9 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Resolving challenges in deep learning-based analyses of histopathological images using explanation methods
Hägele, M., Seegerer, P., Lapuschkin, S., Bockmayr, M., Samek, W., Klauschen, F., Müller, K-R. & Binder, A., 14.04.2020, In: SCI REP-UK. 10, 1, p. 6423Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Progressive or relapsed Burkitt lymphoma or leukemia in children and adolescents after BFM-type first-line therapy
Woessmann, W., Zimmermann, M., Meinhardt, A., Müller, S., Hauch, H., Knörr, F., Oschlies, I., Klapper, W., Niggli, F., Kabickova, E., Attarbaschi, A., Reiter, A. & Burkhardt, B., 02.04.2020, In: BLOOD. 135, 14, p. 1124-1132 9 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
genBaRcode - a comprehensive R package for genetic barcode analysis
Thielecke, L., Cornils, K. & Glauche, I., 01.04.2020, In: BIOINFORMATICS. 36, 7, p. 2189-2194 6 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Effects of the growth pattern of medulloblastoma on short-term neurological impairments after surgery: results from the prospective multicenter HIT-SIOP PNET 4 study
Schepke, E., Tisell, M., Kennedy, C., Puget, S., Ferroli, P., Chevignard, M., Doz, F., Pizer, B., Rutkowski, S., Massimino, M., Navajas, A., Schwalbe, E., Hicks, D., Clifford, S. C., Pietsch, T. & Lannering, B., 04.2020, In: Journal of neurosurgery. Pediatrics. p. 1-9 9 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
EGFRvIII upregulates DNA mismatch repair resulting in increased temozolomide sensitivity of MGMT promoter methylated glioblastoma
Struve, N., Binder, Z. A., Stead, L. F., Brend, T., Bagley, S. J., Faulkner, C., Ott, L., Müller-Goebel, J., Weik, A-S., Hoffer, K., Krug, L., Rieckmann, T., Bußmann, L., Henze, M., Morrissette, J. J. D., Kurian, K. M., Schüller, U., Petersen, C., Rothkamm, K., O Rourke, D. M., Short, S. C. & Kriegs, M., 04.2020, In: ONCOGENE. 39, 15, p. 3041-3055 15 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Germline Elongator mutations in Sonic Hedgehog medulloblastoma
Waszak, S. M., Robinson, G. W., Gudenas, B. L., Smith, K. S., Forget, A., Kojic, M., Garcia-Lopez, J., Hadley, J., Hamilton, K. V., Indersie, E., Buchhalter, I., Kerssemakers, J., Jäger, N., Sharma, T., Rausch, T., Kool, M., Sturm, D., Jones, D. T. W., Vasilyeva, A., Tatevossian, R. G., Neale, G., Lombard, B., Loew, D., Nakitandwe, J., Rusch, M., Bowers, D. C., Bendel, A., Partap, S., Chintagumpala, M., Crawford, J., Gottardo, N. G., Smith, A., Dufour, C., Rutkowski, S., Eggen, T., Wesenberg, F., Kjaerheim, K., Feychting, M., Lannering, B., Schüz, J., Johansen, C., Andersen, T. V., Röösli, M., Kuehni, C. E., Grotzer, M., Remke, M., Puget, S., Pajtler, K. W., Milde, T., Witt, O., Ryzhova, M., Korshunov, A., Orr, B. A., Ellison, D. W., Brugieres, L., Lichter, P., Nichols, K. E., Gajjar, A., Wainwright, B. J., Ayrault, O., Korbel, J. O., Northcott, P. A. & Pfister, S. M., 04.2020, In: NATURE. 580, 7803, p. 396-401 6 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Hemophagocytic lymphohistiocytosis in adults: collaborative analysis of 137 cases of a nationwide German registry
Birndt, S., Schenk, T., Heinevetter, B., Brunkhorst, F. M., Maschmeyer, G., Rothmann, F., Weber, T., Müller, M., Panse, J., Penack, O., Schroers, R., Braess, J., Frickhofen, N., Ehl, S., Janka, G., Lehmberg, K., Pletz, M. W., Hochhaus, A., Ernst, T. & La Rosée, P., 04.2020, In: J CANCER RES CLIN. 146, 4, p. 1065-1077 13 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Hyperferritinemia in Critically Ill Patients
Lachmann, G., Knaak, C., Vorderwülbecke, G., La Rosée, P., Balzer, F., Schenk, T., Schuster, F. S., Nyvlt, P., Janka, G., Brunkhorst, F. M., Keh, D. & Spies, C., 04.2020, In: CRIT CARE MED. 48, 4, p. 459-465 7 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Synovial sarcoma disease characteristics and primary tumor sites differ between patient age groups: a report of the Cooperative Weichteilsarkom Studiengruppe (CWS)
Scheer, M., Blank, B., Bauer, S., Vokuhl, C., Stegmaier, S., Feuchtgruber, S., Henssen, A., Sparber-Sauer, M., Eggert, A., Handgretinger, R., Pekrun, A., Rossig, C., Rutkowski, S., Schlegel, P-G., Schrappe, M., Simon, T., Kazanowska, B., Niggli, F., Ladenstein, R., Ljungman, G., Jahnukainen, K., Fuchs, J., Bielack, S. S., Koscielniak, E., Klingebiel, T. & Cooperative Weichteilsarkom Studiengruppe [CWS], 04.2020, In: J CANCER RES CLIN. 146, 4, p. 953-960 8 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
hGFAP-Positive Stem Cells Depend on Brg1 for Proper Formation of Cerebral and Cerebellar Structures
Holdhof, D., Schoof, M., Hellwig, M., Holdhof, N. H., Niesen, J. & Schüller, U., 14.03.2020, In: CEREB CORTEX. 30, 3, p. 1382-1392 11 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Molecular profiling of an osseous metastasis in glioblastoma during checkpoint inhibition: potential mechanisms of immune escape
Mohme, M., Maire, C. L., Schliffke, S., Joosse, S. A., Alawi, M., Matschke, J., Schüller, U., Dierlamm, J., Martens, T., Pantel, K., Riethdorf, S., Lamszus, K. & Westphal, M., 09.03.2020, In: ACTA NEUROPATHOL COM. 8, 1, 28.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Returning to daily life: a qualitative interview study on parents of childhood cancer survivors in Germany
Peikert, M. L., Inhestern, L., Krauth, K. A., Escherich, G., Rutkowski, S., Kandels, D. & Bergelt, C., 08.03.2020, In: BMJ OPEN. 10, 3, p. e033730Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
A multi-omics approach reveals mechanisms of nanomaterial toxicity and structure-activity relationships in alveolar macrophages
Bannuscher, A., Karkossa, I., Buhs, S., Nollau, P., Kettler, K., Balas, M., Dinischiotu, A., Hellack, B., Wiemann, M., Luch, A., von Bergen, M., Haase, A. & Schubert, K., 03.2020, In: NANOTOXICOLOGY. 14, 2, p. 181-195 15 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Cerebrospinal fluid evaluation in adult patients with medulloblastoma
von Bueren, A. O., Hagel, C. & Rutkowski, S., 03.2020, In: LANCET ONCOL. 21, 3, p. e120Research output: SCORING: Contribution to journal › Other (editorial matter etc.) › Research
Treatment and outcome of IG-MYC+ neoplasms with precursor B-cell phenotype in childhood and adolescence
Herbrueggen, H., Mueller, S., Rohde, J., Arias Padilla, L., Moericke, A., Attarbaschi, A., Zimmermann, M., Ratei, R., Brueggemann, M., Siebert, R., Goehring, G., Schlegelberger, B., Bradtke, J., Klapper, W., Woessmann, W. & Burkhardt, B., 03.2020, In: LEUKEMIA. 34, 3, p. 942-946 5 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Desmoplastic myxoid tumor, SMARCB1-mutant: clinical, histopathological and molecular characterization of a pineal region tumor encountered in adolescents and adults
Thomas, C., Wefers, A., Bens, S., Nemes, K., Agaimy, A., Oyen, F., Vogelgesang, S., Rodriguez, F. J., Brett, F. M., McLendon, R., Bodi, I., Burel-Vandenbos, F., Keyvani, K., Tippelt, S., Poulsen, F. R., Lipp, E. S., Giannini, C., Reifenberger, G., Kuchelmeister, K., Pietsch, T., Kordes, U., Siebert, R., Frühwald, M. C., Johann, P. D., Sill, M., Kool, M., von Deimling, A., Paulus, W. & Hasselblatt, M., 02.2020, In: ACTA NEUROPATHOL. 139, 2, p. 277-286 10 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Genome-wide analysis of acute leukemia and clonally related histiocytic sarcoma in a series of three pediatric patients
Bleeke, M., Johann, P., Gröbner, S., Alten, J., Cario, G., Schäfer, H., Klapper, W., Khoury, J., Pfister, S. & Müller, I., 02.2020, In: PEDIATR BLOOD CANCER. 67, 2, p. e28074Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Hematopoietic stem cell transplantation for children with acute myeloid leukemia-results of the AML SCT-BFM 2007 trial
Sauer, M. G., Lang, P. J., Albert, M. H., Bader, P., Creutzig, U., Eyrich, M., Greil, J., Gruhn, B., Holter, W., Klingebiel, T., Kremens, B., von der Leyen, H., Mauz-Körholz, C., Meisel, R., Mischke, K., Müller, I., Niemeyer, C. M., Peters, C., Pohler, C., Reinhardt, D., Burkhardt, B., Schlegel, P. G., Schulz, A. S., Schrum, J., Sedlacek, P., Strahm, B., Woessmann, W., Handgretinger, R., Zimmermann, M. & Borkhardt, A., 02.2020, In: LEUKEMIA. 34, 2, p. 613-624 12 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Molecular characterization of histopathological ependymoma variants
Neumann, J. E., Spohn, M., Obrecht, D., Mynarek, M., Thomas, C., Hasselblatt, M., Dorostkar, M. M., Wefers, A. K., Frank, S., Monoranu, C-M., Koch, A., Witt, H., Kool, M., Pajtler, K. W., Rutkowski, S., Glatzel, M. & Schüller, U., 02.2020, In: ACTA NEUROPATHOL. 139, 2, p. 305-318 14 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Molecular subgrouping of primary pineal parenchymal tumors reveals distinct subtypes correlated with clinical parameters and genetic alterations
Pfaff, E., Aichmüller, C., Sill, M., Stichel, D., Snuderl, M., Karajannis, M. A., Schuhmann, M. U., Schittenhelm, J., Hasselblatt, M., Thomas, C., Korshunov, A., Rhizova, M., Wittmann, A., Kaufhold, A., Iskar, M., Ketteler, P., Lohmann, D., Orr, B. A., Ellison, D. W., von Hoff, K., Mynarek, M., Rutkowski, S., Sahm, F., von Deimling, A., Lichter, P., Kool, M., Zapatka, M., Pfister, S. M. & Jones, D. T. W., 02.2020, In: ACTA NEUROPATHOL. 139, 2, p. 243-257 15 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Social inequalities in the participation and activity of children and adolescents with leukemia, brain tumors, and sarcomas (SUPATEEN): a protocol for a multicenter longitudinal prospective observational study
Roick, J., Berner, R., Bernig, T., Erdlenbruch, B., Escherich, G., Faber, J., Klein, C., Bochennek, K., Kratz, C., Kühr, J., Längler, A., Lode, H. N., Metzler, M., Müller, H., Reinhardt, D., Sauerbrey, A., Schepper, F., Scheurlen, W., Schneider, D., Schwabe, G. C. & Richter, M., 31.01.2020, In: BMC PEDIATR. 20, 1, p. 48Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Evidence for the Misfolding of the A1 Domain within Multimeric von Willebrand Factor in Type 2 von Willebrand Disease
Tischer, A., Brehm, M. A., Machha, V. R., Moon-Tasson, L., Benson, L. M., Nelton, K. J., Leger, R. R., Obser, T., Martinez-Vargas, M., Whitten, S. T., Chen, D., Pruthi, R. K., Bergen, H. R., Cruz, M. A., Schneppenheim, R. & Auton, M., 17.01.2020, In: J MOL BIOL. 432, 2, p. 305-323 19 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Ulceration in Prolidase Deficiency: Successful Treatment with Anticoagulants
Süßmuth, K., Metze, D., Muresan, A-M., Lehmberg, K., Zur Stadt, U., Speckmann, C., Park, J. H., Marquardt, T., Oji, V. & Goerge, T., 07.01.2020, In: ACTA DERM-VENEREOL. 100, 1, p. adv00002Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Comprehensive assessments and related interventions to enhance the long-term outcomes of child, adolescent and young adult cancer survivors - presentation of the CARE for CAYA-Program study protocol and associated literature review
Salchow, J., Mann, J., Koch, B., von Grundherr, J., Jensen, W., Elmers, S., Straub, L. A., Vettorazzi, E., Escherich, G., Rutkowski, S., Dwinger, S., Bergelt, C., Sokalska-Duhme, M., Bielack, S., Calaminus, G., Baust, K., Classen, C. F., Rössig, C., Faber, J., Faller, H., Hilgendorf, I., Gebauer, J., Langer, T., Metzler, M., Schuster, S., Niemeyer, C., Puzik, A., Reinhardt, D., Dirksen, U., Sander, A., Köhler, M., Habermann, J. K., Bokemeyer, C. & Stein, A., 06.01.2020, In: BMC CANCER. 20, 1, p. 16Research output: SCORING: Contribution to journal › SCORING: Review article › Research
Germline GPR161 Mutations Predispose to Pediatric Medulloblastoma
Begemann, M., Waszak, S. M., Robinson, G. W., Jäger, N., Sharma, T., Knopp, C., Kraft, F., Moser, O., Mynarek, M., Guerrini-Rousseau, L., Brugieres, L., Varlet, P., Pietsch, T., Bowers, D. C., Chintagumpala, M., Sahm, F., Korbel, J. O., Rutkowski, S., Eggermann, T., Gajjar, A., Northcott, P., Elbracht, M., Pfister, S. M., Kontny, U. & Kurth, I., 01.01.2020, In: J CLIN ONCOL. 38, 1, p. 43-50 8 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Acute impact of an endurance race on cardiac function and biomarkers of myocardial injury in triathletes with and without myocardial fibrosis
Tahir, E., Scherz, B., Starekova, J., Muellerleile, K., Fischer, R., Schoennagel, B., Warncke, M., Stehning, C., Cavus, E., Bohnen, S., Radunski, U. K., Blankenberg, S., Simon, P., Pressler, A., Adam, G., Patten, M. & Lund, G. K., 01.2020, In: EUR J PREV CARDIOL. 27, 1, p. 94-104 11 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Distinct molecular response patterns of activating STAT3 mutations associate with penetrance of lymphoproliferation and autoimmunity
Jägle, S., Heeg, M., Grün, S., Rensing-Ehl, A., Maccari, M. E., Klemann, C., Jones, N., Lehmberg, K., Bettoni, C., Warnatz, K., Grimbacher, B., Biebl, A., Schauer, U., Hague, R., Neth, O., Mauracher, A., Pachlopnik Schmid, J., Fabre, A., Kostyuchenko, L., Führer, M., Lorenz, M. R., Schwarz, K., Rohr, J. & Ehl, S., 01.2020, In: CLIN IMMUNOL. 210, p. 108316Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review