Department of Pediatric Hematology and Oncology

Publications

  1. 2020
  2. Stem Cell Transplantation and Vinblastine Monotherapy for Relapsed Pediatric Anaplastic Large Cell Lymphoma: Results of the International, Prospective ALCL-Relapse Trial

    Knörr, F., Brugières, L., Pillon, M., Zimmermann, M., Ruf, S., Attarbaschi, A., Mellgren, K., Burke, G. A. A., Uyttebroeck, A., Wróbel, G., Beishuizen, A., Aladjidi, N., Reiter, A. & Woessmann, W., 01.12.2020, In: J CLIN ONCOL. 38, 34, p. 3999-4009 11 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  3. Molecular characterization of CNS paragangliomas identifies cauda equina paragangliomas as a distinct tumor entity

    Schweizer, L., Thierfelder, F., Thomas, C., Soschinski, P., Suwala, A., Stichel, D., Wefers, A. K., Wessels, L., Misch, M., Kim, H-Y., Jödicke, R., Teichmann, D., Kaul, D., Kahn, J., Bockmayr, M., Hasselblatt, M., Younsi, A., Unterberg, A., Knie, B., Walter, J., Al Safatli, D., May, S-A., Jödicke, A., Ntoulias, G., Moskopp, D., Vajkoczy, P., Heppner, F. L., Capper, D., Hartmann, W., Hartmann, C., von Deimling, A., Reuss, D. E., Schöler, A. & Koch, A., 12.2020, In: ACTA NEUROPATHOL. 140, 6, p. 893-906 14 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  4. Mucopolysaccharidosis type I due to maternal uniparental disomy of chromosome 4 with partial isodisomy of 4p16.3p15.2

    Kloth, K., Vater, I., Lindschau, R., Rau, I., Caliebe, A. & Muschol, N. M., 12.2020, In: MOL GENET METAB REP. 25, 100660.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  5. Treatment response of CNS high-grade neuroepithelial tumors with MN1 alteration

    Baroni, L. V., Rugilo, C., Lubieniecki, F., Sampor, C., Freytes, C., Nobre, L., Hansford, J. R., Malalasekera, V. S., Zapotocky, M., Dodgshun, A., Martinez, O. C., La Madrid, A. M., Lavarino, C., Suñol, M., Rutkowski, S., Schuller, U., Bouffet, E., Ramaswamy, V. & Alderete, D., 12.2020, In: PEDIATR BLOOD CANCER. 67, 12, p. e28627

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  6. Ependymomas in infancy: underlying genetic alterations, histological features, and clinical outcome

    Jünger, S. T., Andreiuolo, F., Mynarek, M., Dörner, E., Zur Mühlen, A., Rutkowski, S., von Bueren, A. O. & Pietsch, T., 11.2020, In: CHILD NERV SYST. 36, 11, p. 2693-2700 8 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  7. Impact of COVID-19 pandemic on mental health of patients with inherited bleeding disorders in Germany

    von Mackensen, S., Halimeh, S., Siebert, M., Wermes, C., Hassenpflug, W., Holstein, K. & Olivieri, M., 11.2020, In: HAEMOPHILIA. 26, 6, p. e272-e281

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  8. Glioma escape signature and clonal development under immune pressure

    Maire, C. L., Mohme, M., Bockmayr, M., Fita, K. D., Riecken, K., Börnigen, D., Alawi, M., Failla, A. V., Kolbe, K., Zapf, S., Holz, M., Neumann, K., Dührsen, L., Lange, T., Fehse, B., Westphal, M. & Lamszus, K., 01.10.2020, In: J CLIN INVEST. 130, 10, p. 5257-5271 15 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  9. IL10RA modulates crizotinib sensitivity in NPM1-ALK+ anaplastic large cell lymphoma

    Prokoph, N., Probst, N. A., Lee, L. C., Monahan, J. M., Matthews, J. D., Liang, H-C., Bahnsen, K., Montes-Mojarro, I. A., Karaca Atabay, E., Sharma, G. G., Malik, V., Larose, H., Forde, S. D., Ducray, S. P., Lobello, C., Wang, Q., Luan, S-L., Pospisilova, S., Gambacorti-Passerini, C. B., Burke, A., Pervez, S., Attarbaschi, A., Janikova, A., Pacquement, H., Landman-Parker, J., Lambilliotte, A., Schleiermacher, G., Klapper, W., Jauch, R., Woessmann, W., Vassal, G., Kenner, L., Merkel, O., Mologni, L., Chiarle, R., Brugieres, L., Geoerger, B., Barbieri, I. & Turner, S. D., 01.10.2020, In: BLOOD. 136, 14, p. 1657-1669 13 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  10. A second cohort of CHD3 patients expands the molecular mechanisms known to cause Snijders Blok-Campeau syndrome

    Drivas, T. G., Li, D., Nair, D., Alaimo, J. T., Alders, M., Altmüller, J., Barakat, T. S., Bebin, E. M., Bertsch, N. L., Blackburn, P. R., Blesson, A., Bouman, A. M., Brockmann, K., Brunelle, P., Burmeister, M., Cooper, G. M., Denecke, J., Dieux-Coëslier, A., Dubbs, H., Ferrer, A., Gal, D., Bartik, L. E., Gunderson, L. B., Hasadsri, L., Jain, M., Karimov, C., Keena, B., Klee, E. W., Kloth, K., Lace, B., Macchiaiolo, M., Marcadier, J. L., Milunsky, J. M., Napier, M. P., Ortiz-Gonzalez, X. R., Pichurin, P. N., Pinner, J., Powis, Z., Prasad, C., Radio, F. C., Rasmussen, K. J., Renaud, D. L., Rush, E. T., Saunders, C., Selcen, D., Seman, A. R., Shinde, D. N., Smith, E. D., Smol, T., Snijders Blok, L., Stoler, J. M., Tang, S., Tartaglia, M., Thompson, M. L., van de Kamp, J. M., Wang, J., Weise, D., Weiss, K., Woitschach, R., Wollnik, B., Yan, H., Zackai, E. H., Zampino, G., Campeau, P. & Bhoj, E., 10.2020, In: EUR J HUM GENET. 28, 10, p. 1422-1431 10 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  11. Comparison of von Willebrand factor platelet-binding activity assays: ELISA overreads type 2B with loss of HMW multimers

    Szederjesi, A., Baronciani, L., Budde, U., Castaman, G., Colpani, P., Lawrie, A. S., Liu, Y., Montgomery, R., Peyvandi, F., Schneppenheim, R., Patzke, J. & Bodó, I., 10.2020, In: J THROMB HAEMOST. 18, 10, p. 2513-2523 11 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  12. Fear of progression in parents of childhood cancer survivors: A Dyadic data analysis

    Peikert, M. L., Inhestern, L., Krauth, K. A., Escherich, G., Rutkowski, S., Kandels, D. & Bergelt, C., 10.2020, In: PSYCHO-ONCOLOGY. 29, 10, p. 1678-1685 8 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  13. Heterogeneous phenotypes in families with duplications of the paternal allele within the imprinting center 1 (H19/IGF2:TSS-DMR) in 11p15.5

    Eggermann, T., Kraft, F., Kloth, K., Klopocki, E., Hüning, I., Hempel, M. & Kunstmann, E., 10.2020, In: CLIN GENET. 98, 4, p. 418-419 2 p.

    Research output: SCORING: Contribution to journalOther (editorial matter etc.)Research

  14. Leukemia-induced dysfunctional TIM-3+CD4+ bone marrow T cells increase risk of relapse in pediatric B-precursor ALL patients

    Blaeschke, F., Willier, S., Stenger, D., Lepenies, M., Horstmann, M. A., Escherich, G., Zimmermann, M., Rojas Ringeling, F., Canzar, S., Kaeuferle, T., Rohlfs, M., Binder, V., Klein, C. & Feuchtinger, T., 10.2020, In: LEUKEMIA. 34, 10, p. 2607-2620 14 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  15. Multiclass cancer classification in fresh frozen and formalin-fixed paraffin-embedded tissue by DigiWest multiplex protein analysis

    Bockmayr, T., Erdmann, G., Treue, D., Jurmeister, P., Schneider, J., Arndt, A., Heim, D., Bockmayr, M., Sachse, C. & Klauschen, F., 10.2020, In: LAB INVEST. 100, 10, p. 1288-1299 12 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  16. Successful Stem Cell Apheresis Using Spectra Optia in a 6 kg Child With Atypical Teratoid/Rhabdoid Tumor

    Brust, P., Schubert, C., Blohm, M. & Winkler, B., 10.2020, In: J PEDIAT HEMATOL ONC. 42, 7, p. e692-e695

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  17. Treosulfan-fludarabine-thiotepa-based conditioning treatment before allogeneic hematopoietic stem cell transplantation for pediatric patients with hematological malignancies

    Kalwak, K., Mielcarek, M., Patrick, K., Styczynski, J., Bader, P., Corbacioglu, S., Burkhardt, B., Sykora, K. W., Drabko, K., Gozdzik, J., Fagioli, F., Greil, J., Gruhn, B., Beier, R., Locatelli, F., Müller, I., Schlegel, P. G., Sedlacek, P., Stachel, K. D., Hemmelmann, C., Möller, A-K., Baumgart, J. & Vora, A., 10.2020, In: BONE MARROW TRANSPL. 55, 10, p. 1996-2007 12 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  18. Long-term cognitive deficits in pediatric low-grade glioma (LGG) survivors reflect pretreatment conditions-report from the German LGG studies

    Traunwieser, T., Kandels, D., Pauls, F., Pietsch, T., Warmuth-Metz, M., Bison, B., Krauss, J., Kortmann, R-D., Timmermann, B., Thomale, U-W., Luettich, P., Neumann-Holbeck, A., Tischler, T., Hernáiz Driever, P., Witt, O. & Gnekow, A. K., 25.09.2020, In: NEURO-ONCOL ADV. 2, 1, vdaa094.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  19. Prognostic Factors in Childhood Anaplastic Large Cell Lymphoma: Long Term Results of the International ALCL99 Trial

    Mussolin, L., Le Deley, M-C., Carraro, E., Damm-Welk, C., Attarbaschi, A., Williams, D., Burke, A., Horibe, K., Nakazawa, A., Wrobel, G., Mann, G., Csóka, M., Uyttebroeck, A., Fernández-Delgado Cerdá, R. F-D., Beishuizen, A., Mellgren, K., Burkhardt, B., Klapper, W., Turner, S. D., D'Amore, E. S. G., Lamant, L., Reiter, A., Woessmann, W., Brugières, L. & Pillon, M. P. O. B. O. T. E. I-G. F. C. N-H. L., 24.09.2020, In: CANCERS. 12, 10

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  20. Platelet adhesion and aggregate formation controlled by immobilised and soluble VWF

    Schneider, M. F., Fallah, M. A., Mess, C., Obser, T., Schneppenheim, R., Alexander-Katz, A., Schneider, S. W. & Huck, V., 11.09.2020, In: BMC MOL CELL BIOL. 21, 1, p. 64

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  21. Chromatin accessibility landscape of pediatric T-lymphoblastic leukemia and human T-cell precursors

    Erarslan-Uysal, B., Kunz, J. B., Rausch, T., Richter-Pechańska, P., van Belzen, I. A., Frismantas, V., Bornhauser, B., Ordoñez-Rueada, D., Paulsen, M., Benes, V., Stanulla, M., Schrappe, M., Cario, G., Escherich, G., Bakharevich, K., Kirschner-Schwabe, R., Eckert, C., Loukanov, T., Gorenflo, M., Waszak, S. M., Bourquin, J-P., Muckenthaler, M. U., Korbel, J. O. & Kulozik, A. E., 07.09.2020, In: EMBO MOL MED. 12, 9, p. e12104

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  22. Early clinical course after hematopoietic stem cell transplantation in children with juvenile metachromatic leukodystrophy

    Beschle, J., Döring, M., Kehrer, C., Raabe, C., Bayha, U., Strölin, M., Böhringer, J., Bevot, A., Kaiser, N., Bender, B., Grimm, A., Lang, P., Müller, I., Krägeloh-Mann, I. & Groeschel, S., 03.09.2020, In: Molecular and cellular pediatrics. 7, 1, p. 12

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  23. Bleeding symptoms in patients diagnosed as type 3 von Willebrand disease: Results from 3WINTERS-IPS, an international and collaborative cross-sectional study

    Tosetto, A., Badiee, Z., Baghaipour, M-R., Baronciani, L., Battle, J., Berntorp, E., Bodó, I., Budde, U., Castaman, G., Eikenboom, J. C. J., Eshghi, P., Ettorre, C., Goodeve, A., Goudemand, J., Hay, C. R. M., Hoorfar, H., Karimi, M., Keikhaei, B., Lassila, R., Leebeek, F. W. G., Lopez Fernandez, M. F., Mannucci, P. M., Mazzucconi, M. G., Morfini, M., Oldenburg, J., Peake, I., Parra Lòpez, R., Peyvandi, F., Schneppenheim, R., Tiede, A., Toogeh, G., Trossaert, M., Zekavat, O., Zetterberg, E. M. K. & Federici, A. B., 09.2020, In: J THROMB HAEMOST. 18, 9, p. 2145-2154 10 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  24. CDKN2A deletion in supratentorial ependymoma with RELA alteration indicates a dismal prognosis: a retrospective analysis of the HIT ependymoma trial cohort

    Jünger, S. T., Andreiuolo, F., Mynarek, M., Wohlers, I., Rahmann, S., Klein-Hitpass, L., Dörner, E., Zur Mühlen, A., Velez-Char, N., von Hoff, K., Warmuth-Metz, M., Kortmann, R-D., Timmermann, B., von Bueren, A., Rutkowski, S. & Pietsch, T., 09.2020, In: ACTA NEUROPATHOL. 140, 3, p. 405-407 3 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  25. Experience with provisional WHO-entities large B-cell lymphoma with IRF4-rearrangement and Burkitt-like lymphoma with 11q aberration in paediatric patients of the NHL-BFM group

    Au-Yeung, R. K. H., Arias Padilla, L., Zimmermann, M., Oschlies, I., Siebert, R., Woessmann, W., Burkhardt, B. & Klapper, W., 09.2020, In: BRIT J HAEMATOL. 190, 5, p. 753-763 11 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  26. Risk factors for mixed chimerism in children with hemophagocytic lymphohistiocytosis after reduced toxicity conditioning

    Wustrau, K., Greil, J., Sykora, K-W., Albert, M. H., Burkhardt, B., Lang, P., Meisel, R., Wössmann, W., Beier, R., Schulz, A., Bader, P., Chada, M., Kühl, J-S., Schlegel, P-G., Speckmann, C., Gruhn, B., Seidel, M., Wawer, A., Ozga, A-K., Janka, G., Ehl, S., Müller, I. & Lehmberg, K., 09.2020, In: PEDIATR BLOOD CANCER. 67, 9, p. e28523

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  27. Systematic analysis of the human tumor cell binding to human vs. murine E- and P-selectin under static vs. dynamic conditions

    Starzonek, S., Maar, H., Labitzky, V., Wicklein, D., Rossdam, C., Buettner, F. F. R., Wolters-Eisfeld, G., Guengoer, C., Wagener, C., Schumacher, U. & Lange, T., 20.08.2020, In: GLYCOBIOLOGY. 30, 9, p. 695-709 15 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  28. Juvenile Blastic Plasmacytoid Dendritic Cell Neoplasm

    Hayani, K. M., Escherich, G., Koch, K., French, L. E. & Wolff, H. H., 18.08.2020, In: ACTA DERM-VENEREOL. 100, 15, p. adv00245

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  29. Stem cell transplantation for children with hemophagocytic lymphohistiocytosis: results from the HLH-2004 study

    Bergsten, E., Horne, A., Hed Myrberg, I., Aricó, M., Astigarraga, I., Ishii, E., Janka, G., Ladisch, S., Lehmberg, K., McClain, K. L., Minkov, M., Nanduri, V., Rosso, D. A., Sieni, E., Winiarski, J. & Henter, J-I., 11.08.2020, In: BLOOD ADV. 4, 15, p. 3754-3766 13 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  30. Neuroinflammatory Disease as an Isolated Manifestation of Hemophagocytic Lymphohistiocytosis

    Blincoe, A., Heeg, M., Campbell, P. K., Hines, M., Khojah, A., Klein-Gitelman, M., Talano, J-A., Speckmann, C., Touzot, F., Lankester, A., Legger, G. E., Rivière, J. G., Garcia-Prat, M., Alonso, L., Putti, M. C., Lehmberg, K., Maier, S., El Chazli, Y., Elmaksoud, M. A., Astigarraga, I., Kurjane, N., Bulina, I., Kenina, V., Bryceson, Y., Rascon, J., Lortie, A., Goldstein, G., Booth, C., Worth, A., Wassmer, E., Schmitt, E. G., Warren, J. T., Bednarski, J. J., Ali, S., Chiang, K-Y., Krueger, J., Henry, M. M., Holland, S. M., Marsh, R. A., Ehl, S. & Haddad, E., 08.2020, In: J CLIN IMMUNOL. 40, 6, p. 901-916 16 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  31. Rare non-Hodgkin lymphoma of childhood and adolescence: A consensus diagnostic and therapeutic approach to pediatric-type follicular lymphoma, marginal zone lymphoma, and nonanaplastic peripheral T-cell lymphoma

    Attarbaschi, A., Abla, O., Arias Padilla, L., Beishuizen, A., Burke, G. A. A., Brugières, L., Bruneau, J., Burkhardt, B., d'Amore, E. S. G., Klapper, W., Kontny, U., Pillon, M., Taj, M., Turner, S. D., Uyttebroeck, A., Woessmann, W. & Mellgren, K., 08.2020, In: PEDIATR BLOOD CANCER. 67, 8, p. e28416

    Research output: SCORING: Contribution to journalSCORING: Review articleResearch

  32. DNA binds to a specific site of the adhesive blood-protein von Willebrand factor guided by electrostatic interactions

    Sandoval-Pérez, A., Berger, R. M. L., Garaizar, A., Farr, S. E., Brehm, M. A., König, G., Schneider, S. W., Collepardo-Guevara, R., Huck, V., Rädler, J. O. & Aponte-Santamaría, C., 27.07.2020, In: NUCLEIC ACIDS RES. 48, 13, p. 7333-7344 12 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  33. Age and DNA-methylation subgroup as potential independent risk factors for treatment stratification in children with Atypical Teratoid/Rhabdoid Tumors (ATRT)

    Frühwald, M. C., Hasselblatt, M., Nemes, K., Bens, S., Steinbügl, M., Johann, P. D., Kerl, K., Hauser, P., Quiroga, E., Solano-Paez, P., Biassoni, V., Gil-da-Costa, M. J., Perek-Polnik, M., van de Wetering, M., Sumerauer, D., Pears, J., Stabell, N., Holm, S., Hengartner, H., Gerber, N. U., Grotzer, M., Boos, J., Ebinger, M., Tippelt, S., Paulus, W., Furtwängler, R., Hernáiz-Driever, P., Reinhard, H., Rutkowski, S., Schlegel, P-G., Schmid, I., Kortmann, R-D., Timmermann, B., Warmuth-Metz, M., Kordes, U., Gerss, J., Nysom, K., Schneppenheim, R., Siebert, R., Kool, M. & Graf, N., 07.07.2020, In: NEURO-ONCOLOGY. 22, 7, p. 1006–1017 12 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  34. Genome-wide DNA methylation profiles distinguish silent from non-silent ACTH adenomas

    Ricklefs, F. L., Fita, K. D., Rotermund, R., Piffko, A., Schmid, S., Capper, D., Buslei, R., Buchfelder, M., Burkhardt, T., Matschke, J., Lamszus, K., Westphal, M., Schüller, U. & Flitsch, J., 07.2020, In: ACTA NEUROPATHOL. 140, 1, p. 95-97 3 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  35. Incidence of SCID in Germany from 2014 to 2015 an ESPED* Survey on Behalf of the API*** Erhebungseinheit für Seltene Pädiatrische Erkrankungen in Deutschland (German Paediatric Surveillance Unit) ** Arbeitsgemeinschaft Pädiatrische Immunologie

    Shai, S., Perez-Becker, R., Andres, O., Bakhtiar, S., Bauman, U., von Bernuth, H., Classen, C-F., Dückers, G., El-Helou, S. M., Gangfuß, A., Ghosh, S., Grimbacher, B., Hauck, F., Hoenig, M., Husain, R. A., Kindle, G., Kipfmueller, F., Klemann, C., Krüger, R., Lainka, E., Lehmberg, K., Lohrmann, F., Morbach, H., Naumann-Bartsch, N., Oommen, P. T., Schulz, A., Seidemann, K., Speckmann, C., Sykora, K-W., von Kries, R. & Niehues, T., 07.2020, In: J CLIN IMMUNOL. 40, 5, p. 708-717 10 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  36. Infant high grade gliomas comprise multiple subgroups characterized by novel targetable gene fusions and favorable outcomes

    Clarke, M., Mackay, A., Ismer, B., Pickles, J. C., Tatevossian, R. G., Newman, S., Bale, T. A., Stoler, I., Izquierdo, E., Temelso, S., Carvalho, D. M., Molinari, V., Burford, A., Howell, L., Virasami, A., Fairchild, A. R., Avery, A., Chalker, J., Kristiansen, M., Haupfear, K., Dalton, J. D., Orisme, W., Wen, J., Hubank, M., Kurian, K. M., Rowe, C., Maybury, M., Crosier, S., Knipstein, J., Schuller, U., Kordes, U., Kram, D. E., Snuderl, M., Bridges, L., Martin, A. J., Doey, L. J., Al-Sarraj, S., Chandler, C., Zebian, B., Cairns, C., Natrajan, R., Boult, J. K., Robinson, S. P., Sill, M., Dunkel, I. J., Gilheeney, S. W., Rosenblum, M. K., Hughes, D., Proszek, P. Z., MacDonald, T. J., Preusser, M., Haberler, C., Slavc, I., Packer, R., Ng, H-K., Caspi, S., Popovic, M., Faganel Kotnik, B., Wood, M. D., Baird, L., Davare, M. A., Solomon, D. A., Olsen, T. K., Brandal, P., Farrell, M., Cryan, J. B., Capra, M., Karremann, M., Schittenhelm, J., Schuhmann, M. U., Ebinger, M., Dinjens, W. N. M., Kerl, K., Hettmer, S., Pietsch, T., Andreiuolo, F., Driever, P. H., Korshunov, A., Hiddingh, L., Worst, B. C., Sturm, D., Zuckermann, M., Witt, O., Bloom, T., Mitchell, C., Miele, E., Colafati, G. S., Diomedi-Camassei, F., Bailey, S., Moore, A. S., Hassall, T. E., Lowis, S. P., Tsoli, M., Cowley, M. J., Ziegler, D. S., Karajannis, M. A., Aquilina, K., Hargrave, D. R., Carceller, F., Marshall, L. V., von Deimling, A., Kramm, C. M., Pfister, S. M., Sahm, F., Baker, S. J., Mastronuzzi, A., Carai, A., Vinci, M., Capper, D., Popov, S., Ellison, D. W., Jacques, T. S., Jones, D. T. W. & Jones, C., 07.2020, In: CANCER DISCOV. 10, 7, p. 942-963 22 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  37. Nonmetastatic Medulloblastoma of Early Childhood: Results From the Prospective Clinical Trial HIT-2000 and An Extended Validation Cohort

    Mynarek, M., von Hoff, K., Pietsch, T., Ottensmeier, H., Warmuth-Metz, M., Bison, B., Pfister, S., Korshunov, A., Sharma, T., Jaeger, N., Ryzhova, M., Zheludkova, O., Golanov, A., Rushing, E. J., Hasselblatt, M., Koch, A., Schüller, U., von Deimling, A., Sahm, F., Sill, M., Riemenschneider, M. J., Dohmen, H., Monoranu, C. M., Sommer, C., Staszewski, O., Mawrin, C., Schittenhelm, J., Brück, W., Filipski, K., Hartmann, C., Meinhardt, M., Pietschmann, K., Haberler, C., Slavc, I., Gerber, N. U., Grotzer, M., Benesch, M., Schlegel, P. G., Deinlein, F., von Bueren, A. O., Friedrich, C., Juhnke, B-O., Obrecht, D., Fleischhack, G., Kwiecien, R., Faldum, A., Kortmann, R. D., Kool, M. & Rutkowski, S., 20.06.2020, In: J CLIN ONCOL. 38, 18, p. 2028-2040 13 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  38. Flash survey on severe acute respiratory syndrome coronavirus-2 infections in paediatric patients on anticancer treatment

    Hrusak, O., Kalina, T., Wolf, J., Balduzzi, A., Provenzi, M., Rizzari, C., Rives, S., Del Pozo Carlavilla, M., Alonso, M. E. V., Domínguez-Pinilla, N., Bourquin, J-P., Schmiegelow, K., Attarbaschi, A., Grillner, P., Mellgren, K., van der Werff Ten Bosch, J., Pieters, R., Brozou, T., Borkhardt, A., Escherich, G., Lauten, M., Stanulla, M., Smith, O., Yeoh, A. E. J., Elitzur, S., Vora, A., Li, C-K., Ariffin, H., Kolenova, A., Dallapozza, L., Farah, R., Lazic, J., Manabe, A., Styczynski, J., Kovacs, G., Ottoffy, G., Felice, M. S., Buldini, B., Conter, V., Stary, J. & Schrappe, M., 06.2020, In: EUR J CANCER. 132, p. 11-16 6 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  39. Hemophagocytic Lymphohistiocytosis in Critically Ill Patients

    Knaak, C., Schuster, F. S., Spies, C., Vorderwülbecke, G., Nyvlt, P., Schenk, T., Balzer, F., La Rosée, P., Janka, G., Brunkhorst, F. M., Keh, D. & Lachmann, G., 06.2020, In: SHOCK. 53, 6, p. 701-709 9 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  40. Influence of anti-thymocyte globulin plasma levels on outcome parameters in stem cell transplanted children

    Vogelsang, V., Kruchen, A., Wustrau, K., Spohn, M. & Müller, I., 06.2020, In: INT IMMUNOPHARMACOL. 83, p. 106371

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  41. The basic helix-loop-helix transcription factor TCF4 impacts brain architecture as well as neuronal morphology and differentiation

    Schoof, M., Hellwig, M., Harrison, L., Holdhof, D., Lauffer, M. C., Niesen, J., Virdi, S., Indenbirken, D. & Schüller, U., 06.2020, In: EUR J NEUROSCI. 51, 11, p. 2219-2235 17 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  42. Can we optimise doxorubicin treatment regimens for children with cancer? Pharmacokinetic simulations and a Delphi consensus procedure

    Siebel, C., Würthwein, G., Lanvers-Kaminsky, C., André, N., Berthold, F., Castelli, I., Chastagner, P., Doz, F., English, M., Escherich, G., Frühwald, M. C., Graf, N., Groll, A. H., Ruggiero, A., Hempel, G. & Boos, J., 28.05.2020, In: BMC PHARMACOL TOXICO. 21, 1, p. 37

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  43. Hemophagocytic lymphohistiocytosis in critically ill patients: diagnostic reliability of HLH-2004 criteria and HScore

    Knaak, C., Nyvlt, P., Schuster, F. S., Spies, C., Heeren, P., Schenk, T., Balzer, F., La Rosée, P., Janka, G., Brunkhorst, F. M., Keh, D. & Lachmann, G., 24.05.2020, In: CRIT CARE. 24, 1, p. 244

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  44. Targeted busulfan-based reduced-intensity conditioning and HLA-matched HSCT cure hemophagocytic lymphohistiocytosis

    Felber, M., Steward, C. G., Kentouche, K., Fasth, A., Wynn, R. F., Zeilhofer, U., Haunerdinger, V., Volkmer, B., Prader, S., Gruhn, B., Ehl, S., Lehmberg, K., Müller, D., Gennery, A. R., Albert, M. H., Hauck, F., Rao, K., Veys, P., Hassan, M., Lankester, A. C., Schmid, J. P., Hauri-Hohl, M. M. & Güngör, T., 12.05.2020, In: BLOOD ADV. 4, 9, p. 1998-2010 13 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  45. Pik3ca mutations significantly enhance the growth of Shh medulloblastoma and lead to metastatic tumour growth in a novel mouse model

    Niesen, J., Ohli, J., Sedlacik, J., Dührsen, L., Hellwig, M., Spohn, M., Holsten, T. & Schüller, U., 01.05.2020, In: CANCER LETT. 477, p. 10-18 9 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  46. An 8-Year-Old Girl with Posterior Fossa Mass

    Ruf, V. C., Schöler, A., Capper, D., Arzberger, T., Herms, J. & Schüller, U., 05.2020, In: BRAIN PATHOL. 30, 3, p. 713-714 2 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  47. Epigenetics impacts upon prognosis and clinical management of choroid plexus tumors

    Thomas, C., Metrock, K., Kordes, U., Hasselblatt, M. & Dhall, G., 05.2020, In: J NEURO-ONCOL. 148, 1, p. 39-45 7 p.

    Research output: SCORING: Contribution to journalSCORING: Review articleResearch

  48. Macrophage-tumor cell interaction promotes ATRT progression and chemoresistance

    Melcher, V., Graf, M., Interlandi, M., Moreno, N., de Faria, F. W., Kim, S. N., Kastrati, D., Korbanka, S., Alfert, A., Gerß, J., Meyer Zu Hörste, G., Hartmann, W., Frühwald, M. C., Dugas, M., Schüller, U., Hasselblatt, M., Albert, T. K. & Kerl, K., 05.2020, In: ACTA NEUROPATHOL. 139, 5, p. 913-936 24 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  49. Preferential sensitivity to HDAC inhibitors in tumors with CREBBP mutation

    Hellwig, M., Merk, D. J., Lutz, B. & Schüller, U., 05.2020, In: CANCER GENE THER. 27, 5, p. 294-300 7 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  50. Register und Studien in der Gesellschaft für Pädiatrische Onkologie und Hämatologie (GPOH) – Welchen Beitrag leisten sie zum Fortschritt?

    Klingebiel, T., Jürgens, H., Glauche, I., Gnekow, A., Kandels, D., Woessmann, W., Schneider, D. T. & Suttorp, M., 05.2020, In: KLIN PADIATR. 232, 3, p. 124-135 12 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

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