Department of Pediatric Hematology and Oncology
Publications
- 2020
Stem Cell Transplantation and Vinblastine Monotherapy for Relapsed Pediatric Anaplastic Large Cell Lymphoma: Results of the International, Prospective ALCL-Relapse Trial
Knörr, F., Brugières, L., Pillon, M., Zimmermann, M., Ruf, S., Attarbaschi, A., Mellgren, K., Burke, G. A. A., Uyttebroeck, A., Wróbel, G., Beishuizen, A., Aladjidi, N., Reiter, A. & Woessmann, W., 01.12.2020, In: J CLIN ONCOL. 38, 34, p. 3999-4009 11 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Molecular characterization of CNS paragangliomas identifies cauda equina paragangliomas as a distinct tumor entity
Schweizer, L., Thierfelder, F., Thomas, C., Soschinski, P., Suwala, A., Stichel, D., Wefers, A. K., Wessels, L., Misch, M., Kim, H-Y., Jödicke, R., Teichmann, D., Kaul, D., Kahn, J., Bockmayr, M., Hasselblatt, M., Younsi, A., Unterberg, A., Knie, B., Walter, J., Al Safatli, D., May, S-A., Jödicke, A., Ntoulias, G., Moskopp, D., Vajkoczy, P., Heppner, F. L., Capper, D., Hartmann, W., Hartmann, C., von Deimling, A., Reuss, D. E., Schöler, A. & Koch, A., 12.2020, In: ACTA NEUROPATHOL. 140, 6, p. 893-906 14 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Mucopolysaccharidosis type I due to maternal uniparental disomy of chromosome 4 with partial isodisomy of 4p16.3p15.2
Kloth, K., Vater, I., Lindschau, R., Rau, I., Caliebe, A. & Muschol, N. M., 12.2020, In: MOL GENET METAB REP. 25, 100660.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Treatment response of CNS high-grade neuroepithelial tumors with MN1 alteration
Baroni, L. V., Rugilo, C., Lubieniecki, F., Sampor, C., Freytes, C., Nobre, L., Hansford, J. R., Malalasekera, V. S., Zapotocky, M., Dodgshun, A., Martinez, O. C., La Madrid, A. M., Lavarino, C., Suñol, M., Rutkowski, S., Schuller, U., Bouffet, E., Ramaswamy, V. & Alderete, D., 12.2020, In: PEDIATR BLOOD CANCER. 67, 12, p. e28627Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Ependymomas in infancy: underlying genetic alterations, histological features, and clinical outcome
Jünger, S. T., Andreiuolo, F., Mynarek, M., Dörner, E., Zur Mühlen, A., Rutkowski, S., von Bueren, A. O. & Pietsch, T., 11.2020, In: CHILD NERV SYST. 36, 11, p. 2693-2700 8 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Impact of COVID-19 pandemic on mental health of patients with inherited bleeding disorders in Germany
von Mackensen, S., Halimeh, S., Siebert, M., Wermes, C., Hassenpflug, W., Holstein, K. & Olivieri, M., 11.2020, In: HAEMOPHILIA. 26, 6, p. e272-e281Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Glioma escape signature and clonal development under immune pressure
Maire, C. L., Mohme, M., Bockmayr, M., Fita, K. D., Riecken, K., Börnigen, D., Alawi, M., Failla, A. V., Kolbe, K., Zapf, S., Holz, M., Neumann, K., Dührsen, L., Lange, T., Fehse, B., Westphal, M. & Lamszus, K., 01.10.2020, In: J CLIN INVEST. 130, 10, p. 5257-5271 15 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
IL10RA modulates crizotinib sensitivity in NPM1-ALK+ anaplastic large cell lymphoma
Prokoph, N., Probst, N. A., Lee, L. C., Monahan, J. M., Matthews, J. D., Liang, H-C., Bahnsen, K., Montes-Mojarro, I. A., Karaca Atabay, E., Sharma, G. G., Malik, V., Larose, H., Forde, S. D., Ducray, S. P., Lobello, C., Wang, Q., Luan, S-L., Pospisilova, S., Gambacorti-Passerini, C. B., Burke, A., Pervez, S., Attarbaschi, A., Janikova, A., Pacquement, H., Landman-Parker, J., Lambilliotte, A., Schleiermacher, G., Klapper, W., Jauch, R., Woessmann, W., Vassal, G., Kenner, L., Merkel, O., Mologni, L., Chiarle, R., Brugieres, L., Geoerger, B., Barbieri, I. & Turner, S. D., 01.10.2020, In: BLOOD. 136, 14, p. 1657-1669 13 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
A second cohort of CHD3 patients expands the molecular mechanisms known to cause Snijders Blok-Campeau syndrome
Drivas, T. G., Li, D., Nair, D., Alaimo, J. T., Alders, M., Altmüller, J., Barakat, T. S., Bebin, E. M., Bertsch, N. L., Blackburn, P. R., Blesson, A., Bouman, A. M., Brockmann, K., Brunelle, P., Burmeister, M., Cooper, G. M., Denecke, J., Dieux-Coëslier, A., Dubbs, H., Ferrer, A., Gal, D., Bartik, L. E., Gunderson, L. B., Hasadsri, L., Jain, M., Karimov, C., Keena, B., Klee, E. W., Kloth, K., Lace, B., Macchiaiolo, M., Marcadier, J. L., Milunsky, J. M., Napier, M. P., Ortiz-Gonzalez, X. R., Pichurin, P. N., Pinner, J., Powis, Z., Prasad, C., Radio, F. C., Rasmussen, K. J., Renaud, D. L., Rush, E. T., Saunders, C., Selcen, D., Seman, A. R., Shinde, D. N., Smith, E. D., Smol, T., Snijders Blok, L., Stoler, J. M., Tang, S., Tartaglia, M., Thompson, M. L., van de Kamp, J. M., Wang, J., Weise, D., Weiss, K., Woitschach, R., Wollnik, B., Yan, H., Zackai, E. H., Zampino, G., Campeau, P. & Bhoj, E., 10.2020, In: EUR J HUM GENET. 28, 10, p. 1422-1431 10 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Comparison of von Willebrand factor platelet-binding activity assays: ELISA overreads type 2B with loss of HMW multimers
Szederjesi, A., Baronciani, L., Budde, U., Castaman, G., Colpani, P., Lawrie, A. S., Liu, Y., Montgomery, R., Peyvandi, F., Schneppenheim, R., Patzke, J. & Bodó, I., 10.2020, In: J THROMB HAEMOST. 18, 10, p. 2513-2523 11 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Fear of progression in parents of childhood cancer survivors: A Dyadic data analysis
Peikert, M. L., Inhestern, L., Krauth, K. A., Escherich, G., Rutkowski, S., Kandels, D. & Bergelt, C., 10.2020, In: PSYCHO-ONCOLOGY. 29, 10, p. 1678-1685 8 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Heterogeneous phenotypes in families with duplications of the paternal allele within the imprinting center 1 (H19/IGF2:TSS-DMR) in 11p15.5
Eggermann, T., Kraft, F., Kloth, K., Klopocki, E., Hüning, I., Hempel, M. & Kunstmann, E., 10.2020, In: CLIN GENET. 98, 4, p. 418-419 2 p.Research output: SCORING: Contribution to journal › Other (editorial matter etc.) › Research
Leukemia-induced dysfunctional TIM-3+CD4+ bone marrow T cells increase risk of relapse in pediatric B-precursor ALL patients
Blaeschke, F., Willier, S., Stenger, D., Lepenies, M., Horstmann, M. A., Escherich, G., Zimmermann, M., Rojas Ringeling, F., Canzar, S., Kaeuferle, T., Rohlfs, M., Binder, V., Klein, C. & Feuchtinger, T., 10.2020, In: LEUKEMIA. 34, 10, p. 2607-2620 14 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Multiclass cancer classification in fresh frozen and formalin-fixed paraffin-embedded tissue by DigiWest multiplex protein analysis
Bockmayr, T., Erdmann, G., Treue, D., Jurmeister, P., Schneider, J., Arndt, A., Heim, D., Bockmayr, M., Sachse, C. & Klauschen, F., 10.2020, In: LAB INVEST. 100, 10, p. 1288-1299 12 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Successful Stem Cell Apheresis Using Spectra Optia in a 6 kg Child With Atypical Teratoid/Rhabdoid Tumor
Brust, P., Schubert, C., Blohm, M. & Winkler, B., 10.2020, In: J PEDIAT HEMATOL ONC. 42, 7, p. e692-e695Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Treosulfan-fludarabine-thiotepa-based conditioning treatment before allogeneic hematopoietic stem cell transplantation for pediatric patients with hematological malignancies
Kalwak, K., Mielcarek, M., Patrick, K., Styczynski, J., Bader, P., Corbacioglu, S., Burkhardt, B., Sykora, K. W., Drabko, K., Gozdzik, J., Fagioli, F., Greil, J., Gruhn, B., Beier, R., Locatelli, F., Müller, I., Schlegel, P. G., Sedlacek, P., Stachel, K. D., Hemmelmann, C., Möller, A-K., Baumgart, J. & Vora, A., 10.2020, In: BONE MARROW TRANSPL. 55, 10, p. 1996-2007 12 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Long-term cognitive deficits in pediatric low-grade glioma (LGG) survivors reflect pretreatment conditions-report from the German LGG studies
Traunwieser, T., Kandels, D., Pauls, F., Pietsch, T., Warmuth-Metz, M., Bison, B., Krauss, J., Kortmann, R-D., Timmermann, B., Thomale, U-W., Luettich, P., Neumann-Holbeck, A., Tischler, T., Hernáiz Driever, P., Witt, O. & Gnekow, A. K., 25.09.2020, In: NEURO-ONCOL ADV. 2, 1, vdaa094.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Prognostic Factors in Childhood Anaplastic Large Cell Lymphoma: Long Term Results of the International ALCL99 Trial
Mussolin, L., Le Deley, M-C., Carraro, E., Damm-Welk, C., Attarbaschi, A., Williams, D., Burke, A., Horibe, K., Nakazawa, A., Wrobel, G., Mann, G., Csóka, M., Uyttebroeck, A., Fernández-Delgado Cerdá, R. F-D., Beishuizen, A., Mellgren, K., Burkhardt, B., Klapper, W., Turner, S. D., D'Amore, E. S. G., Lamant, L., Reiter, A., Woessmann, W., Brugières, L. & Pillon, M. P. O. B. O. T. E. I-G. F. C. N-H. L., 24.09.2020, In: CANCERS. 12, 10Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Platelet adhesion and aggregate formation controlled by immobilised and soluble VWF
Schneider, M. F., Fallah, M. A., Mess, C., Obser, T., Schneppenheim, R., Alexander-Katz, A., Schneider, S. W. & Huck, V., 11.09.2020, In: BMC MOL CELL BIOL. 21, 1, p. 64Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Chromatin accessibility landscape of pediatric T-lymphoblastic leukemia and human T-cell precursors
Erarslan-Uysal, B., Kunz, J. B., Rausch, T., Richter-Pechańska, P., van Belzen, I. A., Frismantas, V., Bornhauser, B., Ordoñez-Rueada, D., Paulsen, M., Benes, V., Stanulla, M., Schrappe, M., Cario, G., Escherich, G., Bakharevich, K., Kirschner-Schwabe, R., Eckert, C., Loukanov, T., Gorenflo, M., Waszak, S. M., Bourquin, J-P., Muckenthaler, M. U., Korbel, J. O. & Kulozik, A. E., 07.09.2020, In: EMBO MOL MED. 12, 9, p. e12104Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Early clinical course after hematopoietic stem cell transplantation in children with juvenile metachromatic leukodystrophy
Beschle, J., Döring, M., Kehrer, C., Raabe, C., Bayha, U., Strölin, M., Böhringer, J., Bevot, A., Kaiser, N., Bender, B., Grimm, A., Lang, P., Müller, I., Krägeloh-Mann, I. & Groeschel, S., 03.09.2020, In: Molecular and cellular pediatrics. 7, 1, p. 12Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Bleeding symptoms in patients diagnosed as type 3 von Willebrand disease: Results from 3WINTERS-IPS, an international and collaborative cross-sectional study
Tosetto, A., Badiee, Z., Baghaipour, M-R., Baronciani, L., Battle, J., Berntorp, E., Bodó, I., Budde, U., Castaman, G., Eikenboom, J. C. J., Eshghi, P., Ettorre, C., Goodeve, A., Goudemand, J., Hay, C. R. M., Hoorfar, H., Karimi, M., Keikhaei, B., Lassila, R., Leebeek, F. W. G., Lopez Fernandez, M. F., Mannucci, P. M., Mazzucconi, M. G., Morfini, M., Oldenburg, J., Peake, I., Parra Lòpez, R., Peyvandi, F., Schneppenheim, R., Tiede, A., Toogeh, G., Trossaert, M., Zekavat, O., Zetterberg, E. M. K. & Federici, A. B., 09.2020, In: J THROMB HAEMOST. 18, 9, p. 2145-2154 10 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
CDKN2A deletion in supratentorial ependymoma with RELA alteration indicates a dismal prognosis: a retrospective analysis of the HIT ependymoma trial cohort
Jünger, S. T., Andreiuolo, F., Mynarek, M., Wohlers, I., Rahmann, S., Klein-Hitpass, L., Dörner, E., Zur Mühlen, A., Velez-Char, N., von Hoff, K., Warmuth-Metz, M., Kortmann, R-D., Timmermann, B., von Bueren, A., Rutkowski, S. & Pietsch, T., 09.2020, In: ACTA NEUROPATHOL. 140, 3, p. 405-407 3 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Experience with provisional WHO-entities large B-cell lymphoma with IRF4-rearrangement and Burkitt-like lymphoma with 11q aberration in paediatric patients of the NHL-BFM group
Au-Yeung, R. K. H., Arias Padilla, L., Zimmermann, M., Oschlies, I., Siebert, R., Woessmann, W., Burkhardt, B. & Klapper, W., 09.2020, In: BRIT J HAEMATOL. 190, 5, p. 753-763 11 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Risk factors for mixed chimerism in children with hemophagocytic lymphohistiocytosis after reduced toxicity conditioning
Wustrau, K., Greil, J., Sykora, K-W., Albert, M. H., Burkhardt, B., Lang, P., Meisel, R., Wössmann, W., Beier, R., Schulz, A., Bader, P., Chada, M., Kühl, J-S., Schlegel, P-G., Speckmann, C., Gruhn, B., Seidel, M., Wawer, A., Ozga, A-K., Janka, G., Ehl, S., Müller, I. & Lehmberg, K., 09.2020, In: PEDIATR BLOOD CANCER. 67, 9, p. e28523Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Systematic analysis of the human tumor cell binding to human vs. murine E- and P-selectin under static vs. dynamic conditions
Starzonek, S., Maar, H., Labitzky, V., Wicklein, D., Rossdam, C., Buettner, F. F. R., Wolters-Eisfeld, G., Guengoer, C., Wagener, C., Schumacher, U. & Lange, T., 20.08.2020, In: GLYCOBIOLOGY. 30, 9, p. 695-709 15 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Juvenile Blastic Plasmacytoid Dendritic Cell Neoplasm
Hayani, K. M., Escherich, G., Koch, K., French, L. E. & Wolff, H. H., 18.08.2020, In: ACTA DERM-VENEREOL. 100, 15, p. adv00245Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Stem cell transplantation for children with hemophagocytic lymphohistiocytosis: results from the HLH-2004 study
Bergsten, E., Horne, A., Hed Myrberg, I., Aricó, M., Astigarraga, I., Ishii, E., Janka, G., Ladisch, S., Lehmberg, K., McClain, K. L., Minkov, M., Nanduri, V., Rosso, D. A., Sieni, E., Winiarski, J. & Henter, J-I., 11.08.2020, In: BLOOD ADV. 4, 15, p. 3754-3766 13 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Neuroinflammatory Disease as an Isolated Manifestation of Hemophagocytic Lymphohistiocytosis
Blincoe, A., Heeg, M., Campbell, P. K., Hines, M., Khojah, A., Klein-Gitelman, M., Talano, J-A., Speckmann, C., Touzot, F., Lankester, A., Legger, G. E., Rivière, J. G., Garcia-Prat, M., Alonso, L., Putti, M. C., Lehmberg, K., Maier, S., El Chazli, Y., Elmaksoud, M. A., Astigarraga, I., Kurjane, N., Bulina, I., Kenina, V., Bryceson, Y., Rascon, J., Lortie, A., Goldstein, G., Booth, C., Worth, A., Wassmer, E., Schmitt, E. G., Warren, J. T., Bednarski, J. J., Ali, S., Chiang, K-Y., Krueger, J., Henry, M. M., Holland, S. M., Marsh, R. A., Ehl, S. & Haddad, E., 08.2020, In: J CLIN IMMUNOL. 40, 6, p. 901-916 16 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Rare non-Hodgkin lymphoma of childhood and adolescence: A consensus diagnostic and therapeutic approach to pediatric-type follicular lymphoma, marginal zone lymphoma, and nonanaplastic peripheral T-cell lymphoma
Attarbaschi, A., Abla, O., Arias Padilla, L., Beishuizen, A., Burke, G. A. A., Brugières, L., Bruneau, J., Burkhardt, B., d'Amore, E. S. G., Klapper, W., Kontny, U., Pillon, M., Taj, M., Turner, S. D., Uyttebroeck, A., Woessmann, W. & Mellgren, K., 08.2020, In: PEDIATR BLOOD CANCER. 67, 8, p. e28416Research output: SCORING: Contribution to journal › SCORING: Review article › Research
DNA binds to a specific site of the adhesive blood-protein von Willebrand factor guided by electrostatic interactions
Sandoval-Pérez, A., Berger, R. M. L., Garaizar, A., Farr, S. E., Brehm, M. A., König, G., Schneider, S. W., Collepardo-Guevara, R., Huck, V., Rädler, J. O. & Aponte-Santamaría, C., 27.07.2020, In: NUCLEIC ACIDS RES. 48, 13, p. 7333-7344 12 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Accurate In-Vivo Quantification of CD19 CAR-T Cells after Treatment with Axicabtagene Ciloleucel (Axi-Cel) and Tisagenlecleucel (Tisa-Cel) Using Digital PCR
Badbaran, A., Berger, C., Riecken, K., Kruchen, A., Geffken, M., Müller, I., Kröger, N., Ayuk, F. A. & Fehse, B., 20.07.2020, In: CANCERS. 12, 7Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Age and DNA-methylation subgroup as potential independent risk factors for treatment stratification in children with Atypical Teratoid/Rhabdoid Tumors (ATRT)
Frühwald, M. C., Hasselblatt, M., Nemes, K., Bens, S., Steinbügl, M., Johann, P. D., Kerl, K., Hauser, P., Quiroga, E., Solano-Paez, P., Biassoni, V., Gil-da-Costa, M. J., Perek-Polnik, M., van de Wetering, M., Sumerauer, D., Pears, J., Stabell, N., Holm, S., Hengartner, H., Gerber, N. U., Grotzer, M., Boos, J., Ebinger, M., Tippelt, S., Paulus, W., Furtwängler, R., Hernáiz-Driever, P., Reinhard, H., Rutkowski, S., Schlegel, P-G., Schmid, I., Kortmann, R-D., Timmermann, B., Warmuth-Metz, M., Kordes, U., Gerss, J., Nysom, K., Schneppenheim, R., Siebert, R., Kool, M. & Graf, N., 07.07.2020, In: NEURO-ONCOLOGY. 22, 7, p. 1006–1017 12 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Genome-wide DNA methylation profiles distinguish silent from non-silent ACTH adenomas
Ricklefs, F. L., Fita, K. D., Rotermund, R., Piffko, A., Schmid, S., Capper, D., Buslei, R., Buchfelder, M., Burkhardt, T., Matschke, J., Lamszus, K., Westphal, M., Schüller, U. & Flitsch, J., 07.2020, In: ACTA NEUROPATHOL. 140, 1, p. 95-97 3 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Incidence of SCID in Germany from 2014 to 2015 an ESPED* Survey on Behalf of the API*** Erhebungseinheit für Seltene Pädiatrische Erkrankungen in Deutschland (German Paediatric Surveillance Unit) ** Arbeitsgemeinschaft Pädiatrische Immunologie
Shai, S., Perez-Becker, R., Andres, O., Bakhtiar, S., Bauman, U., von Bernuth, H., Classen, C-F., Dückers, G., El-Helou, S. M., Gangfuß, A., Ghosh, S., Grimbacher, B., Hauck, F., Hoenig, M., Husain, R. A., Kindle, G., Kipfmueller, F., Klemann, C., Krüger, R., Lainka, E., Lehmberg, K., Lohrmann, F., Morbach, H., Naumann-Bartsch, N., Oommen, P. T., Schulz, A., Seidemann, K., Speckmann, C., Sykora, K-W., von Kries, R. & Niehues, T., 07.2020, In: J CLIN IMMUNOL. 40, 5, p. 708-717 10 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Infant high grade gliomas comprise multiple subgroups characterized by novel targetable gene fusions and favorable outcomes
Clarke, M., Mackay, A., Ismer, B., Pickles, J. C., Tatevossian, R. G., Newman, S., Bale, T. A., Stoler, I., Izquierdo, E., Temelso, S., Carvalho, D. M., Molinari, V., Burford, A., Howell, L., Virasami, A., Fairchild, A. R., Avery, A., Chalker, J., Kristiansen, M., Haupfear, K., Dalton, J. D., Orisme, W., Wen, J., Hubank, M., Kurian, K. M., Rowe, C., Maybury, M., Crosier, S., Knipstein, J., Schuller, U., Kordes, U., Kram, D. E., Snuderl, M., Bridges, L., Martin, A. J., Doey, L. J., Al-Sarraj, S., Chandler, C., Zebian, B., Cairns, C., Natrajan, R., Boult, J. K., Robinson, S. P., Sill, M., Dunkel, I. J., Gilheeney, S. W., Rosenblum, M. K., Hughes, D., Proszek, P. Z., MacDonald, T. J., Preusser, M., Haberler, C., Slavc, I., Packer, R., Ng, H-K., Caspi, S., Popovic, M., Faganel Kotnik, B., Wood, M. D., Baird, L., Davare, M. A., Solomon, D. A., Olsen, T. K., Brandal, P., Farrell, M., Cryan, J. B., Capra, M., Karremann, M., Schittenhelm, J., Schuhmann, M. U., Ebinger, M., Dinjens, W. N. M., Kerl, K., Hettmer, S., Pietsch, T., Andreiuolo, F., Driever, P. H., Korshunov, A., Hiddingh, L., Worst, B. C., Sturm, D., Zuckermann, M., Witt, O., Bloom, T., Mitchell, C., Miele, E., Colafati, G. S., Diomedi-Camassei, F., Bailey, S., Moore, A. S., Hassall, T. E., Lowis, S. P., Tsoli, M., Cowley, M. J., Ziegler, D. S., Karajannis, M. A., Aquilina, K., Hargrave, D. R., Carceller, F., Marshall, L. V., von Deimling, A., Kramm, C. M., Pfister, S. M., Sahm, F., Baker, S. J., Mastronuzzi, A., Carai, A., Vinci, M., Capper, D., Popov, S., Ellison, D. W., Jacques, T. S., Jones, D. T. W. & Jones, C., 07.2020, In: CANCER DISCOV. 10, 7, p. 942-963 22 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Nonmetastatic Medulloblastoma of Early Childhood: Results From the Prospective Clinical Trial HIT-2000 and An Extended Validation Cohort
Mynarek, M., von Hoff, K., Pietsch, T., Ottensmeier, H., Warmuth-Metz, M., Bison, B., Pfister, S., Korshunov, A., Sharma, T., Jaeger, N., Ryzhova, M., Zheludkova, O., Golanov, A., Rushing, E. J., Hasselblatt, M., Koch, A., Schüller, U., von Deimling, A., Sahm, F., Sill, M., Riemenschneider, M. J., Dohmen, H., Monoranu, C. M., Sommer, C., Staszewski, O., Mawrin, C., Schittenhelm, J., Brück, W., Filipski, K., Hartmann, C., Meinhardt, M., Pietschmann, K., Haberler, C., Slavc, I., Gerber, N. U., Grotzer, M., Benesch, M., Schlegel, P. G., Deinlein, F., von Bueren, A. O., Friedrich, C., Juhnke, B-O., Obrecht, D., Fleischhack, G., Kwiecien, R., Faldum, A., Kortmann, R. D., Kool, M. & Rutkowski, S., 20.06.2020, In: J CLIN ONCOL. 38, 18, p. 2028-2040 13 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Flash survey on severe acute respiratory syndrome coronavirus-2 infections in paediatric patients on anticancer treatment
Hrusak, O., Kalina, T., Wolf, J., Balduzzi, A., Provenzi, M., Rizzari, C., Rives, S., Del Pozo Carlavilla, M., Alonso, M. E. V., Domínguez-Pinilla, N., Bourquin, J-P., Schmiegelow, K., Attarbaschi, A., Grillner, P., Mellgren, K., van der Werff Ten Bosch, J., Pieters, R., Brozou, T., Borkhardt, A., Escherich, G., Lauten, M., Stanulla, M., Smith, O., Yeoh, A. E. J., Elitzur, S., Vora, A., Li, C-K., Ariffin, H., Kolenova, A., Dallapozza, L., Farah, R., Lazic, J., Manabe, A., Styczynski, J., Kovacs, G., Ottoffy, G., Felice, M. S., Buldini, B., Conter, V., Stary, J. & Schrappe, M., 06.2020, In: EUR J CANCER. 132, p. 11-16 6 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Hemophagocytic Lymphohistiocytosis in Critically Ill Patients
Knaak, C., Schuster, F. S., Spies, C., Vorderwülbecke, G., Nyvlt, P., Schenk, T., Balzer, F., La Rosée, P., Janka, G., Brunkhorst, F. M., Keh, D. & Lachmann, G., 06.2020, In: SHOCK. 53, 6, p. 701-709 9 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Influence of anti-thymocyte globulin plasma levels on outcome parameters in stem cell transplanted children
Vogelsang, V., Kruchen, A., Wustrau, K., Spohn, M. & Müller, I., 06.2020, In: INT IMMUNOPHARMACOL. 83, p. 106371Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
The basic helix-loop-helix transcription factor TCF4 impacts brain architecture as well as neuronal morphology and differentiation
Schoof, M., Hellwig, M., Harrison, L., Holdhof, D., Lauffer, M. C., Niesen, J., Virdi, S., Indenbirken, D. & Schüller, U., 06.2020, In: EUR J NEUROSCI. 51, 11, p. 2219-2235 17 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Can we optimise doxorubicin treatment regimens for children with cancer? Pharmacokinetic simulations and a Delphi consensus procedure
Siebel, C., Würthwein, G., Lanvers-Kaminsky, C., André, N., Berthold, F., Castelli, I., Chastagner, P., Doz, F., English, M., Escherich, G., Frühwald, M. C., Graf, N., Groll, A. H., Ruggiero, A., Hempel, G. & Boos, J., 28.05.2020, In: BMC PHARMACOL TOXICO. 21, 1, p. 37Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Hemophagocytic lymphohistiocytosis in critically ill patients: diagnostic reliability of HLH-2004 criteria and HScore
Knaak, C., Nyvlt, P., Schuster, F. S., Spies, C., Heeren, P., Schenk, T., Balzer, F., La Rosée, P., Janka, G., Brunkhorst, F. M., Keh, D. & Lachmann, G., 24.05.2020, In: CRIT CARE. 24, 1, p. 244Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Targeted busulfan-based reduced-intensity conditioning and HLA-matched HSCT cure hemophagocytic lymphohistiocytosis
Felber, M., Steward, C. G., Kentouche, K., Fasth, A., Wynn, R. F., Zeilhofer, U., Haunerdinger, V., Volkmer, B., Prader, S., Gruhn, B., Ehl, S., Lehmberg, K., Müller, D., Gennery, A. R., Albert, M. H., Hauck, F., Rao, K., Veys, P., Hassan, M., Lankester, A. C., Schmid, J. P., Hauri-Hohl, M. M. & Güngör, T., 12.05.2020, In: BLOOD ADV. 4, 9, p. 1998-2010 13 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Pik3ca mutations significantly enhance the growth of Shh medulloblastoma and lead to metastatic tumour growth in a novel mouse model
Niesen, J., Ohli, J., Sedlacik, J., Dührsen, L., Hellwig, M., Spohn, M., Holsten, T. & Schüller, U., 01.05.2020, In: CANCER LETT. 477, p. 10-18 9 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
An 8-Year-Old Girl with Posterior Fossa Mass
Ruf, V. C., Schöler, A., Capper, D., Arzberger, T., Herms, J. & Schüller, U., 05.2020, In: BRAIN PATHOL. 30, 3, p. 713-714 2 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Epigenetics impacts upon prognosis and clinical management of choroid plexus tumors
Thomas, C., Metrock, K., Kordes, U., Hasselblatt, M. & Dhall, G., 05.2020, In: J NEURO-ONCOL. 148, 1, p. 39-45 7 p.Research output: SCORING: Contribution to journal › SCORING: Review article › Research
Macrophage-tumor cell interaction promotes ATRT progression and chemoresistance
Melcher, V., Graf, M., Interlandi, M., Moreno, N., de Faria, F. W., Kim, S. N., Kastrati, D., Korbanka, S., Alfert, A., Gerß, J., Meyer Zu Hörste, G., Hartmann, W., Frühwald, M. C., Dugas, M., Schüller, U., Hasselblatt, M., Albert, T. K. & Kerl, K., 05.2020, In: ACTA NEUROPATHOL. 139, 5, p. 913-936 24 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Preferential sensitivity to HDAC inhibitors in tumors with CREBBP mutation
Hellwig, M., Merk, D. J., Lutz, B. & Schüller, U., 05.2020, In: CANCER GENE THER. 27, 5, p. 294-300 7 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
Register und Studien in der Gesellschaft für Pädiatrische Onkologie und Hämatologie (GPOH) – Welchen Beitrag leisten sie zum Fortschritt?
Klingebiel, T., Jürgens, H., Glauche, I., Gnekow, A., Kandels, D., Woessmann, W., Schneider, D. T. & Suttorp, M., 05.2020, In: KLIN PADIATR. 232, 3, p. 124-135 12 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review