Research ExplorerJournalsMOL THER Publications

MOL THER - Molecular therapy : the journal of the American Society of Gene Therapy

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Publications

  1. 2024

  2. CARs come to AID

    Ayuk, F. & Fehse, B., 03.04.2024, In: MOL THER. 32, 4, p. 861-862 2 p.

    Research output: SCORING: Contribution to journal › Editorial › Research

  3. 2023

  4. Neuroserpin Gene Therapy Inhibits Retinal Ganglion Cell Apoptosis and Promotes Functional Preservation in Glaucoma

    Chitranshi, N., Rajput, R., Godinez, A., Pushpitha, K., Mirzaei, M., Basavarajappa, D., Gupta, V., Sharma, S., You, Y., Galliciotti, G., Salekdeh, G. H., Baker, M., Graham, S. L. & Gupta, V. K., 05.07.2023, In: MOL THER. 31, 7, p. 2056-2076 21 p.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  5. 2022

  6. Identification of New AAV9 Engineered Capsids Targeting Mouse and Monkey Brains Through a Directed Evolution Approach in BALB/c Mice

    Serena, GG., Luoni, M., Bellinazzi, B., Martin, T., Körbelin, J. & Broccoli, V., 07.06.2022, In: MOL THER. 30, 4, p. 209-210 2 p.

    Research output: SCORING: Contribution to journal › Conference abstract in journal › Research › peer-review

  7. Tumor cell E-selectin ligands determine partialefficacy of bortezomib on spontaneous lung metastasis formation of solid human tumors in vivo

    Lange, T., Valentiner, U., Wicklein, D., Maar, H., Labitzky, V., Ahlers, A-K., Starzonek, S., Genduso, S., Staffeldt, L., Pahlow, C., Dück, A-M., Stürken, C., Baranowsky, A., Bauer, A. T., Bulk, E., Schwab, A., Riecken, K., Börnchen, C., Kiefmann, R., Abraham, V., DeLisser, H. M., Gemoll, T., Habermann, J. K., Block, A., Pantel, K. & Schumacher, U., 06.04.2022, In: MOL THER. 30, 4, p. 1536-1552 17 p.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  8. 2021

  9. Two cases of T cell lymphoma following Piggybac-mediated CAR T cell therapy

    Schambach, A., Morgan, M. & Fehse, B., 01.09.2021, In: MOL THER. 29, 9, p. 2631-2633 3 p.

    Research output: SCORING: Contribution to journal › Other (editorial matter etc.) › Research

  10. Identification of New Adeno-Associated Virus 9 (AAV9) Capsid Variants Targeting the BALB/c Mouse Brain through Directed Evolution

    Giannelli, SG., Luoni, M., Conti, E., Niro, A., Trepel, M., Körbelin, J. & Broccoli, V., 17.05.2021, In: MOL THER. 29, 4, p. 149-150 2 p.

    Research output: SCORING: Contribution to journal › Conference abstract in journal › Research › peer-review

  11. 2019

  12. EZH2 Inhibition in Ewing Sarcoma Upregulates G Expression for Targeting with Gene-Modified T Cells

    Kailayangiri, S., Altvater, B., Lesch, S., Balbach, S., Göttlich, C., Kühnemundt, J., Mikesch, J-H., Schelhaas, S., Jamitzky, S., Meltzer, J., Farwick, N., Greune, L., Fluegge, M., Kerl, K., Lode, H. N., Siebert, N., Müller, I., Walles, H., Hartmann, W. & Rossig, C., 08.05.2019, In: MOL THER. 27, 5, p. 933-946 14 p.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  13. 2018

  14. Novel Gene Therapy Approaches for Whole Brain Delivery of the Lysosomal Gcase Enzyme for Wide Protection from Alpha-Synuclein Toxic Aggregates

    Broccoli, V., Ordozza, G., Bido, S., Valtorta, M., Morabito, G., Körbelin, J., Cacellieri, C. & Giannelli, S., 05.2018, In: MOL THER. 26, 5 Suppl., p. 131-131 278.

    Research output: SCORING: Contribution to journal › Conference abstract in journal › Research › peer-review

  15. The Time Is Ripe for Somatic Genome Editing: NIH Program to Strengthen Translation

    Fehse, B. & Abramowski-Mock, U., 07.03.2018, In: MOL THER. 26, 3, p. 671-674 4 p.

    Research output: SCORING: Contribution to journal › Other (editorial matter etc.) › Research

  16. 2017

  17. Brain Endothelial-Targeted Gene Therapy in a Mouse Model of Incontinentia Pigmenti

    Körbelin, J., Dogbevia, G., Töllner, K., Bröer, S., Ridder, D., Grasshoff, H., Brandt, C., Straub, B., Trepel, M., Löscher, W. & Schwaninger, M., 05.2017, In: MOL THER. 25, 5, p. 256-257

    Research output: SCORING: Contribution to journal › Conference abstract in journal › Research › peer-review

  18. Optical Barcoding for Single-Clone Tracking to Study Tumor Heterogeneity

    Mohme, M., Maire, C. L., Riecken, K., Zapf, S., Aranyossy, T., Westphal, M., Lamszus, K. & Fehse, B., 01.03.2017, In: MOL THER. 25, 3, p. 621-633

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  19. 2016

  20. Pulmonary Targeting of Adeno-associated Viral Vectors by Next-generation Sequencing-guided Screening of Random Capsid Displayed Peptide Libraries

    Körbelin, J., Sieber, T., Michelfelder, S., Lunding, L., Spies, E., Hunger, A., Alawi, M., Rapti, K., Indenbirken, D., Müller, O. J., Pasqualini, R., Arap, W., Kleinschmidt, J. A. & Trepel, M., 06.2016, In: MOL THER. 24, 6, p. 1050-61

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  21. 2015

  22. Directed Alternative Splicing in Nijmegen Breakage Syndrome: Proof of Principle Concerning Its Therapeutical Application

    Salewsky, B., Hildebrand, G., Rothe, S., Parplys, A. C., Radszewski, J., Kieslich, M., Wessendorf, P., Krenzlin, H., Borgmann, K., Nussenzweig, A., Sperling, K. & Digweed, M., 12.08.2015, In: MOL THER. 24, 1, p. 117-124

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  23. Intraspinal Delivery of Polyethylene Glycol-coated Gold Nanoparticles Promotes Functional Recovery After Spinal Cord Injury.

    Papastefanaki, F., Jakovcevski, I., Poulia, N., Djogo, N., Schulz, F., Martinovic, T., Ciric, D., Loers, G., Vossmeyer, T., Weller, H., Schachner, M. & Matsas, R., 25.03.2015, In: MOL THER. 23, 6, p. 993-1002

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  24. 2014

  25. Transduction of fetal mice with a feline lentiviral vector induces liver tumors which exhibit an E2F activation signature

    Condiotti, R., Goldenberg, D., Giladi, H., Schnitzer-Perlman, T., Waddington, S. N., Buckley, S. M., Heim, D., Cheung, W., Themis, M., Coutelle, C., Simerzin, A., Osejindu, E., Wege, H., Themis, M. & Galun, E., 01.01.2014, In: MOL THER. 22, 1, p. 59-68 10 p.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  26. 2010

  27. Immune responses to AAV in canine muscle monitored by cellular assays and noninvasive imaging

    Wang, Z., Storb, R., Lee, D., Kushmerick, M. J., Chu, B., Berger, C., Arnett, A., Allen, J., Chamberlain, J. S., Riddell, S. R. & Tapscott, S. J., 03.2010, In: MOL THER. 18, 3, p. 617-24 8 p.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  28. Polysialic acid glycomimetic promotes functional recovery and plasticity after spinal cord injury in mice.

    Mehanna, A., Jakovcevski, I., Acar, A., Xiao, M., Loers, G., Rougon, G., Irintchev, A. & Schachner, M., 2010, In: MOL THER. 18, 1, p. 34-43 1.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  29. The extracellular matrix glycoprotein tenascin-C is beneficial for spinal cord regeneration.

    Chen, J., Lee, H. J., Jakovcevski, I., Shah, R., Bhagat, N., Loers, G., Liu, H-Y., Meiners, S., Taschenberger, G., Kügler, S., Irintchev, A. & Schachner, M., 2010, In: MOL THER. 18, 10, p. 1769-1777 10.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  30. 2009

  31. Cell-intrinsic and Vector-related Properties Cooperate to Determine the Incidence and Consequences of Insertional Mutagenesis

    Bartels, S., 09.2009, In: MOL THER.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  32. Stem cell marking with promotor-deprived self-inactivating retroviral vectors does not lead to induced clonal imbalance.

    Cornils, K., Lange, C., Schambach, A., Brugman, M. H., Nowak, R., Lioznov, M., Baum, C. & Fehse, B., 2009, In: MOL THER. 17, 1, p. 131-143 1.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  33. 2008

  34. A multicolor panel of novel lentiviral "gene ontology" (LeGO) vectors for functional gene analysis

    Weber, K., Bartsch, U., Stocking, C. & Fehse, B., 2008, In: MOL THER. 16, 4, p. 698-706 4.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  35. Gene targeting of mutant COL1A2 alleles in mesenchymal stem cells from individuals with osteogenesis imperfecta.

    Chamberlain, J. R., Deyle, D. R., Schwarze, U., Wang, P., Hirata, R. K., Li, Y., Byers, P. H. & Russell, D. W., 2008, In: MOL THER. 16, 1, p. 187-193 1.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  36. 2007

  37. Bystander killing of malignant glioma by bone marrow-derived tumor-infiltrating progenitor cells expressing a suicide gene.

    Miletic, H., Fischer, Y., Litwak, S., Giroglou, T., Waerzeggers, Y., Winkeler, A., Li, H., Himmelreich, U., Lange, C., Stenzel, W., Deckert, M., Neumann, H., Jacobs, A. H. & von Laer, D., 2007, In: MOL THER. 15, 7, p. 1373-1381 7.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  38. Transfer of autologous gene-modified T cells in HIV-infected patients with advanced immunodeficiency and drug-resistant virus.

    van Lunzen, J., Glaunsinger, T., Stahmer, I., von Baehr, V., Baum, C., Schilz, A., Kuehlcke, K., Naundorf, S., Martinius, H., Hermann, F., Giroglou, T., Newrzela, S., Müller, I., Brauer, F., Brandenburg, G., Alexandrov, A. & von Laer, D., 2007, In: MOL THER. 15, 5, p. 1024-1033 5.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  39. 2006

  40. Cytoglobin overexpression protects against damage-induced fibrosis.

    Xu, R., Harrison, P. M., Chen, M., Li, L., Tsui, T. Y., Fung, P. C. W., Cheung, P., Wang, G., Li, H., Diao, Y., Krissansen, G. W., Xu, S. & Farzaneh, F., 2006, In: MOL THER. 13, 6, p. 1093-1100 6.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  41. 2004

  42. Simplified generation of high-titer retrovirus producer cells for clinically relevant retroviral vectors by reversible inclusion of a lox-P-flanked marker gene

    Loew, R., Selevsek, N., Fehse, B., von Laer, D., Baum, C., Fauser, A. & Kuehlcke, K., 05.2004, In: MOL THER. 9, 5, p. 738-46 9 p.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  43. Chance or necessity? Insertional mutagenesis in gene therapy and its consequences

    Baum, C., von Kalle, C., Staal, F. J. T., Li, Z., Fehse, B., Schmidt, M., Weerkamp, F., Karlsson, S., Wagemaker, G. & Williams, D. A., 01.2004, In: MOL THER. 9, 1, p. 5-13 9 p.

    Research output: SCORING: Contribution to journal › SCORING: Review article › Research

  44. 2002

  45. Upstream conserved sequences of mouse leukemia viruses are important for high transgene expression in lymphoid and hematopoietic cells

    Wahlers, A., Kustikova, O., Zipfel, P. F., Itoh, K., Koester, M., Heberlein, C., Li, Z., Schiedlmeier, B., Skerka, C., Fehse, B. & Baum, C., 09.2002, In: MOL THER. 6, 3, p. 313-320 8 p.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  46. Highly efficient retroviral gene transfer based on centrifugation-mediated vector preloading of tissue culture vessels.

    Kühlcke, K., Fehse, B., Schilz, A., Loges, S., Lindemann, C., Ayuketang Ayuk, F., Lehmann, F., Stute, N., Fauser, A. A., Zander, A. R. & Eckert, H-G., 2002, In: MOL THER. 5, 4, p. 473-478 4.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  47. 2001

  48. Incorporation of tumor-targeting peptides into recombinant adeno-associated virus capsids

    Grifman, M., Trepel, M., Speece, P., Gilbert, L. B., Arap, W., Pasqualini, R. & Weitzman, M. D., 06.2001, In: MOL THER. 3, 6, p. 964-75 12 p.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review

  49. 2000

  50. CD34 splice variant: an attractive marker for selection of gene-modified cells

    Fehse, B., Richters, A., Putimtseva-Scharf, K., Klump, H., Li, Z., Ostertag, W., Zander, A. R. & Baum, C., 05.2000, In: MOL THER. 1, 5 Pt 1, p. 448-456 9 p.

    Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review