MOL THER-NUCL ACIDS - Molecular therapy. Nucleic acids
Publications
- 2019
Long Noncoding RNA-Enriched Vesicles Secreted by Hypoxic Cardiomyocytes Drive Cardiac Fibrosis
Kenneweg, F., Bang, C., Xiao, K., Boulanger, C. M., Loyer, X., Mazlan, S., Schroen, B., Hermans-Beijnsberger, S., Foinquinos, A., Hirt, M. N., Eschenhagen, T., Funcke, S., Stojanovic, S., Genschel, C., Schimmel, K., Just, A., Pfanne, A., Scherf, K., Dehmel, S., Raemon-Buettner, S. M., Fiedler, J. & Thum, T., 06.12.2019, In: MOL THER-NUCL ACIDS. 18, p. 363-374 12 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
- 2018
Transient Retrovirus-Based CRISPR/Cas9 All-in-One Particles for Efficient, Targeted Gene Knockout
Knopp, Y., Geis, F. K., Heckl, D., Horn, S., Neumann, T., Kuehle, J., Meyer, J., Fehse, B., Baum, C., Morgan, M., Meyer, J., Schambach, A. & Galla, M., 07.12.2018, In: MOL THER-NUCL ACIDS. 13, p. 256-274 19 p.Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
- 2017
Evaluation of MYBPC3 trans-Splicing and Gene Replacement as Therapeutic Options in Human iPSC-Derived Cardiomyocytes
Prondzynski, M., Krämer, E., Laufer, S., Domke-Shibamiya, A., Pless, O., Flenner, F., Müller, O. J., Münch, J., Redwood, C., Hansen, A., Patten-Hamel, M., Eschenhagen, T., Mearini, G. & Carrier, L., 05.2017, In: MOL THER-NUCL ACIDS. 7, p. 475-486Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
- 2016
Selection and Characterization of an α6β4 Integrin blocking DNA Aptamer
Berg, K., Lange, T., Mittelberger, F., Schumacher, U. & Hahn, U., 15.03.2016, In: MOL THER-NUCL ACIDS. 5, p. e294Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review
- 2013
Repair of Mybpc3 mRNA by 5'-trans-splicing in a Mouse Model of Hypertrophic Cardiomyopathy
Mearini, G., Stimpel, D., Krämer, E., Geertz, B., Braren, I., Hornung, C., Précigout, G., Müller, O. J., Katus, H. A., Eschenhagen, T., Voit, T., Garcia, L., Lorain, S. & Carrier, L., 01.01.2013, In: MOL THER-NUCL ACIDS. 2, p. e102Research output: SCORING: Contribution to journal › SCORING: Journal article › Research › peer-review