MOL THER-NUCL ACIDS - Molecular therapy. Nucleic acids

Publications

  1. 2019
  2. Long Noncoding RNA-Enriched Vesicles Secreted by Hypoxic Cardiomyocytes Drive Cardiac Fibrosis

    Kenneweg, F., Bang, C., Xiao, K., Boulanger, C. M., Loyer, X., Mazlan, S., Schroen, B., Hermans-Beijnsberger, S., Foinquinos, A., Hirt, M. N., Eschenhagen, T., Funcke, S., Stojanovic, S., Genschel, C., Schimmel, K., Just, A., Pfanne, A., Scherf, K., Dehmel, S., Raemon-Buettner, S. M., Fiedler, J. & Thum, T., 06.12.2019, In: MOL THER-NUCL ACIDS. 18, p. 363-374 12 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  3. 2018
  4. Transient Retrovirus-Based CRISPR/Cas9 All-in-One Particles for Efficient, Targeted Gene Knockout

    Knopp, Y., Geis, F. K., Heckl, D., Horn, S., Neumann, T., Kuehle, J., Meyer, J., Fehse, B., Baum, C., Morgan, M., Meyer, J., Schambach, A. & Galla, M., 07.12.2018, In: MOL THER-NUCL ACIDS. 13, p. 256-274 19 p.

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  5. 2017
  6. Evaluation of MYBPC3 trans-Splicing and Gene Replacement as Therapeutic Options in Human iPSC-Derived Cardiomyocytes

    Prondzynski, M., Krämer, E., Laufer, S., Domke-Shibamiya, A., Pless, O., Flenner, F., Müller, O. J., Münch, J., Redwood, C., Hansen, A., Patten-Hamel, M., Eschenhagen, T., Mearini, G. & Carrier, L., 05.2017, In: MOL THER-NUCL ACIDS. 7, p. 475-486

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  7. 2016
  8. Selection and Characterization of an α6β4 Integrin blocking DNA Aptamer

    Berg, K., Lange, T., Mittelberger, F., Schumacher, U. & Hahn, U., 15.03.2016, In: MOL THER-NUCL ACIDS. 5, p. e294

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review

  9. 2013
  10. Repair of Mybpc3 mRNA by 5'-trans-splicing in a Mouse Model of Hypertrophic Cardiomyopathy

    Mearini, G., Stimpel, D., Krämer, E., Geertz, B., Braren, I., Hornung, C., Précigout, G., Müller, O. J., Katus, H. A., Eschenhagen, T., Voit, T., Garcia, L., Lorain, S. & Carrier, L., 01.01.2013, In: MOL THER-NUCL ACIDS. 2, p. e102

    Research output: SCORING: Contribution to journalSCORING: Journal articleResearchpeer-review