Defibrotide for prophylaxis of hepatic veno-occlusive disease in paediatric haemopoietic stem-cell transplantation: an open-label, phase 3, randomised controlled trial.

  • Selim Corbacioglu
  • Simone Cesaro
  • Maura Faraci
  • Dominique Valteau-Couanet
  • Bernd Gruhn
  • Attilio Rovelli
  • Jaap J Boelens
  • Annette Hewitt
  • Johanna Schrum
  • Ansgar S Schulz
  • Ingo Müller
  • Jerry Stein
  • Robert Wynn
  • Johann Greil
  • Karl-Walter Sykora
  • Susanne Matthes-Martin
  • Monika Führer
  • Anne O'Meara
  • Jacek Toporski
  • Petr Sedlacek
  • Paul G Schlegel
  • Karoline Ehlert
  • Anders Fasth
  • Jacek Winiarski
  • Johan Arvidson
  • Christine Mauz-Körholz
  • Hulya Ozsahin
  • Andre Schrauder
  • Peter Bader
  • Joseph Massaro
  • Ralph D'Agostino
  • Margaret Hoyle
  • Massimo Iacobelli
  • Klaus-Michael Debatin
  • Christina Peters
  • Giorgio Dini

Abstract

Hepatic veno-occlusive disease is a leading cause of morbidity and mortality after haemopoietic stem-cell transplantation (HSCT). We aimed to assess whether defibrotide can reduce the incidence of veno-occlusive disease in this setting.

Bibliografische Daten

OriginalspracheEnglisch
Aufsatznummer9823
ISSN0140-6736
StatusVeröffentlicht - 2012
pubmed 22364685